Strategic biomarkers for drug development in treating rare diseases and diseases in neonates and infants
about
Neonatal drug therapy: The first frontier of therapeutics for children204th ENMC International Workshop on Biomarkers in Duchenne Muscular Dystrophy 24-26 January 2014, Naarden, The NetherlandsRegulatory science needs for neonates: a call for neonatal community collaboration and innovationClinical Pharmacology Studies in Critically Ill Children.Effect of Kidney Function on Drug Kinetics and Dosing in Neonates, Infants, and ChildrenTailored tools to improve pharmacotherapy in infants.Drug development challenges and strategies to address emerging and resistant fungal pathogens.Drugs for rare disorders.Safety, dosing, and pharmaceutical quality for studies that evaluate medicinal products (including biological products) in neonates.Collaboration in Regulatory Science to Facilitate Therapeutic Development for Neonates.Useful pharmacodynamic endpoints in children: selection, measurement, and next steps.Using a meta-narrative literature review and focus groups with key stakeholders to identify perceived challenges and solutions for generating robust evidence on the effectiveness of treatments for rare diseases.
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P2860
Strategic biomarkers for drug development in treating rare diseases and diseases in neonates and infants
description
2013 nî lūn-bûn
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2013 թուականի Ապրիլին հրատարակուած գիտական յօդուած
@hyw
2013 թվականի ապրիլին հրատարակված գիտական հոդված
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2013年の論文
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2013年論文
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2013年論文
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2013年論文
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2013年論文
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2013年論文
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2013年论文
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name
Strategic biomarkers for drug ...... seases in neonates and infants
@ast
Strategic biomarkers for drug ...... seases in neonates and infants
@en
Strategic biomarkers for drug ...... seases in neonates and infants
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type
label
Strategic biomarkers for drug ...... seases in neonates and infants
@ast
Strategic biomarkers for drug ...... seases in neonates and infants
@en
Strategic biomarkers for drug ...... seases in neonates and infants
@nl
prefLabel
Strategic biomarkers for drug ...... seases in neonates and infants
@ast
Strategic biomarkers for drug ...... seases in neonates and infants
@en
Strategic biomarkers for drug ...... seases in neonates and infants
@nl
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Strategic biomarkers for drug ...... seases in neonates and infants
@en
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Bernd Meibohm
Gibert J. Burckart
Hari Cheryl Sachs
Jane P. F. Bai
Jeffrey S. Barrett
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10.1208/S12248-013-9452-Z
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2013-04-01T00:00:00Z
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1010751511