Widespread biochemical correction of murine mucopolysaccharidosis type VII pathology by liver hydrodynamic plasmid delivery.
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Image-Guided Hydrodynamic Gene Delivery: Current Status and Future DirectionsTherapies of mucopolysaccharidosis IVA (Morquio A syndrome).Activities of daily living in patients with Hunter syndrome: impact of enzyme replacement therapy and hematopoietic stem cell transplantation.Liver production of sulfamidase reverses peripheral and ameliorates CNS pathology in mucopolysaccharidosis IIIA mice.TIMP-1 attenuates blood-brain barrier permeability in mice with acute liver failure.Activity of daily living for Morquio A syndrome.Cell microencapsulation: a potential tool for the treatment of neuronopathic lysosomal storage diseases.Gene therapy approaches for lysosomal storage disorders, a good model for the treatment of mendelian diseases.Gene delivery strategies for the treatment of mucopolysaccharidoses.Current and potential therapeutic strategies for mucopolysaccharidoses.High and prolonged sulfamidase secretion by the liver of MPS-IIIA mice following hydrodynamic tail vein delivery of antibiotic-free pFAR4 plasmid vector.Efficient expression of stabilized mRNA PEG-peptide polyplexes in liver.Translational Advances of Hydrofection by Hydrodynamic Injection.
P2860
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P2860
Widespread biochemical correction of murine mucopolysaccharidosis type VII pathology by liver hydrodynamic plasmid delivery.
description
2009 nî lūn-bûn
@nan
2009年の論文
@ja
2009年学术文章
@wuu
2009年学术文章
@zh
2009年学术文章
@zh-cn
2009年学术文章
@zh-hans
2009年学术文章
@zh-my
2009年学术文章
@zh-sg
2009年學術文章
@yue
2009年學術文章
@zh-hant
name
Widespread biochemical correct ...... hydrodynamic plasmid delivery.
@en
Widespread biochemical correct ...... hydrodynamic plasmid delivery.
@nl
type
label
Widespread biochemical correct ...... hydrodynamic plasmid delivery.
@en
Widespread biochemical correct ...... hydrodynamic plasmid delivery.
@nl
prefLabel
Widespread biochemical correct ...... hydrodynamic plasmid delivery.
@en
Widespread biochemical correct ...... hydrodynamic plasmid delivery.
@nl
P2093
P2860
P356
P1433
P1476
Widespread biochemical correct ...... hydrodynamic plasmid delivery.
@en
P2093
P2860
P2888
P304
P356
10.1038/GT.2009.36
P577
2009-04-09T00:00:00Z
P6179
1021955337