Cationic PMMA nanoparticles bind and deliver antisense oligoribonucleotides allowing restoration of dystrophin expression in the mdx mouse - Wikidata - wikimedia - TriplyDB

Cationic PMMA nanoparticles bind and deliver antisense oligoribonucleotides allowing restoration of dystrophin expression in the mdx mouse

Cationic PMMA nanoparticles bind and deliver antisense oligoribonucleotides allowing restoration of dystrophin expression in the mdx mouse

http://www.wikidata.org/entity/Q33713471

about

Nanoparticle delivery of antisense oligonucleotides and their application in the exon skipping strategy for Duchenne muscular dystrophy Emerging genetic therapies to treat Duchenne muscular dystrophy Anti-tumor activity of splice-switching oligonucleotides.Restoring dystrophin expression in duchenne muscular dystrophy muscle progress in exon skipping and stop codon read through.Effective Delivery of PEGylated siRNA-Containing Lipoplexes to Extraperitoneal Tumours following Intraperitoneal Administration.Novel compounds for the treatment of Duchenne muscular dystrophy: emerging therapeutic agents Antisense drug discovery and development.New developments in the use of gene therapy to treat Duchenne muscular dystrophy.Exon-skipping antisense oligonucleotides to correct missplicing in neurogenetic diseases.Pluronic-PEI copolymers enhance exon-skipping of 2'-O-methyl phosphorothioate oligonucleotide in cell culture and dystrophic mdx mice.Antisense Oligonucleotide-Based Therapy for Neuromuscular Disease.Translational development of splice-modifying antisense oligomers.Targeting Splicing in the Treatment of Human Disease Nanotherapy for Duchenne muscular dystrophy.Accurate quantification of dystrophin mRNA and exon skipping levels in duchenne muscular dystrophy.Biodistribution studies of polymeric nanoparticles for drug delivery in mice.Persistent dystrophin protein restoration 90 days after a course of intraperitoneally administered naked 2'OMePS AON and ZM2 NP-AON complexes in mdx mice.Antisense mediated exon skipping therapy for duchenne muscular dystrophy (DMD)Biodistribution and molecular studies on orally administered nanoparticle-AON complexes encapsulated with alginate aiming at inducing dystrophin rescue in mdx mice.Dystrophin restoration in skeletal, heart and skin arrector pili smooth muscle of mdx mice by ZM2 NP-AON complexes.Encapsulation of Piper cabralanum (Piperaceae) nonpolar extract in poly(methyl methacrylate) by miniemulsion and evaluation of increase in the effectiveness of antileukemic activity in K562 cells.

P2860

Q26992271-DF40D6E8-9321-4501-81CA-63C0C592B2A6 Q33796975-94CBF79D-D3D5-4B98-8E91-CBC53F44502F Q34401490-6A7A58B9-8C4D-4C5A-B77B-B3371C2D6879 Q35072755-C67C2027-F844-464B-857E-17A4DAC3D3A4 Q35100812-A48129E2-EE7F-431B-A374-32FB51F26CCE Q36925191-64128828-FC0C-4773-B5B3-A734A3003F78 Q37859009-8E9149C6-CC2B-402E-A227-310F2E28A39D Q38168863-0F0ABEFE-F827-4EFD-8707-FCF73CA61DDF Q38186137-5C3E2019-90C5-4E0C-ADF9-BDEE9FBE0F4C Q38311878-69BEFFEF-5314-4063-8AE3-8AE5789924CD Q38734734-3D192560-89B9-41DB-81E6-424DC9CB8F21 Q38996657-7E745943-AB19-47B6-A247-A9B500A53FC4 Q39154733-A118052C-6E11-498B-9838-4C2AF94C54FD Q39233936-237F648A-B896-4DBF-B35B-BDF51F0212E9 Q39932620-6362F502-76F2-4399-9B53-44AD015A213D Q41773191-ABC17D5E-CFE8-4545-AE99-29B71B715D68 Q41854668-E5D18C85-6BC5-4F7D-A89E-A9BF85947811 Q42122236-C63D2443-1EE2-4564-97FB-03862F9733D2 Q42181611-418E9230-B22A-429F-9466-47DC680CFE7B Q43243962-28146464-1B60-4034-8041-9DFD8EEEB135 Q47161864-8FB89874-75B8-4737-9A07-1DDFBAC0D86D

P2860

Cationic PMMA nanoparticles bind and deliver antisense oligoribonucleotides allowing restoration of dystrophin expression in the mdx mouse

http://www.wikidata.org/entity/Q33713471

description

2009 nî lūn-bûn

@nan

2009 թուականի Փետրուարին հրատարակուած գիտական յօդուած

@hyw

2009 թվականի փետրվարին հրատարակված գիտական հոդված

@hy

2009年の論文

@ja

2009年論文

@yue

2009年論文

@zh-hant

2009年論文

@zh-hk

2009年論文

@zh-mo

2009年論文

@zh-tw

2009年论文

@wuu

name

Cationic PMMA nanoparticles bi ...... in expression in the mdx mouse

@ast

Cationic PMMA nanoparticles bi ...... in expression in the mdx mouse

@en

type

label

Cationic PMMA nanoparticles bi ...... in expression in the mdx mouse

@ast

Cationic PMMA nanoparticles bi ...... in expression in the mdx mouse

@en

prefLabel

Cationic PMMA nanoparticles bi ...... in expression in the mdx mouse

@ast

Cationic PMMA nanoparticles bi ...... in expression in the mdx mouse

@en

P1433

Q33713471-E096BBB8-69D4-4BFE-99B3-BD4B1562EA17

P1476

Q33713471-DF1421A1-EAFD-46CC-AF7A-A548B500B3E7

P2093

Q33713471-1DEBA1C7-EA20-4EBF-90CC-C21AA6621F08

Q33713471-1FB2323E-C1EB-4308-BC6A-5AF3CBA72C19

Q33713471-32DDC080-A186-4222-826C-D2960EFE0961

Q33713471-6455139F-42C7-4170-B074-1C452F81C596

Q33713471-6950598A-A181-4801-8267-D397951564DF

Q33713471-6BE55178-723B-44EF-9FC4-ECE04BD260E9

Q33713471-87ED3E22-5D1A-49CE-9AAB-D55AA57D2639

Q33713471-8C33AB9C-5D59-4472-8395-CCF6EF29B593

Q33713471-A0A37BD9-D6DE-4A6D-BDB6-536F0DE0DC17

Q33713471-B156C7D9-C59F-4DAE-B560-569E55CF1B7E

P2860

Q33713471-0252DC50-972E-4580-83CB-1673A53088A2

Q33713471-07DD3FA0-8B2A-4E80-9AF2-025B63BD229D

Q33713471-09A13F8E-6F66-4B6B-872F-9D02B3B9504B

Q33713471-0F14EC45-E90C-4A80-BFFA-F0477A65D87D

Q33713471-190CFF64-E114-4036-80D2-D7FEB2BE1023

Q33713471-1EFDCAE4-FCC3-4933-BCDB-1A02D6F6DCA4

Q33713471-2A1888A1-6599-4062-83A8-DEC3234DE500

Q33713471-38871A20-F55F-4DC7-AD57-8E4838803BB7

Q33713471-39858E0F-4762-46CD-884A-8A2EFB9A91C9

Q33713471-417C250D-1C0A-474E-9F18-75561DBE0E58

P304

Q33713471-98BB001F-55EB-4A06-8BCF-BE5CA7492E4F

P31

Q33713471-3D81B0A7-9AD0-4B1D-A558-F1B4309C2108

P356

Q33713471-00C925C9-EAE2-465F-BF99-78E7DEB968C8

P433

Q33713471-4053DBFE-C06F-48FC-896C-7B0B2E4B68EA

P478

Q33713471-D9E43205-5958-4786-947E-1070B4379F42

P50

Q33713471-1515B382-F30F-4004-A81B-0C1AA3C87E72

Q33713471-70EA2223-E3E4-4E7F-A895-FAE8578DFE08

Q33713471-759607CA-F9DD-49DD-9D51-F101DC89E453

Q33713471-BC7D8194-3135-45E7-B2CA-959D1B211AFB

Q33713471-D5CE71C3-208D-4EC3-8383-C57868571CE4

Q33713471-D7749941-0181-4705-878C-31A0A29A79B7

Q33713471-DCE38D44-A3A3-4210-906B-CF56672A3759

Q33713471-E8B13867-BB26-4424-A621-3733B67A3E73

Q33713471-F450E6DB-A2B8-447E-A5D6-B51850DE1D66

Q33713471-F4DA05A6-6562-4046-88F7-6BA7D72C21EF

P577

Q33713471-D67B1459-6613-42DF-855A-B2920B2245D3

P5875

Q33713471-06A85A05-2BAD-4E43-88B4-6C202B33FDD2

P698

Q33713471-C7367325-3B8B-4E57-8F0D-026EC4E38C83

P932

Q33713471-7785B41F-49E7-4739-89E7-B8DFE979C9AC

P356

P1433

Molecular Therapy

P1476

Cationic PMMA nanoparticles bi ...... in expression in the mdx mouse

@en

P2093

Alessandra Ferlini

http://www.w3.org/2001/XMLSchema#string

Alessandro Medici

http://www.w3.org/2001/XMLSchema#string

Daniela Perrone

http://www.w3.org/2001/XMLSchema#string

Elena Bassi

http://www.w3.org/2001/XMLSchema#string

Elena Martoni

http://www.w3.org/2001/XMLSchema#string

Francesca Gualandi

http://www.w3.org/2001/XMLSchema#string

Giuliano Tomelleri

http://www.w3.org/2001/XMLSchema#string

Lara Mari

http://www.w3.org/2001/XMLSchema#string

Marcella Neri

http://www.w3.org/2001/XMLSchema#string

Marina Fabris

http://www.w3.org/2001/XMLSchema#string

P2860

Antisense-mediated exon skipping: a versatile tool with therapeutic and research applications

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

Nanopolymers improve delivery of exon skipping oligonucleotides and concomitant dystrophin expression in skeletal muscle of mdx mice.

Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles

Induction of potent immune responses by cationic microparticles with adsorbed human immunodeficiency virus DNA vaccines.

New adjuvants on a polymethylmethacrylate base.

Entries in the Leiden Duchenne muscular dystrophy mutation database: an overview of mutation types and paradoxical cases that confirm the reading-frame rule.

Body-wide gene therapy of Duchenne muscular dystrophy in the mdx mouse model.

Formulation aspects of biodegradable polymeric microspheres for antigen delivery.

Gene expression profiling studies of aging in cardiac and skeletal muscles.

P304

820-827

http://www.w3.org/2001/XMLSchema#string

P31

scholarly article

P356

10.1038/MT.2009.8

http://www.w3.org/2001/XMLSchema#string

P433

5

http://www.w3.org/2001/XMLSchema#string

P478

17

http://www.w3.org/2001/XMLSchema#string

P50

Katia Sparnacci

Matteo Bovolenta

Gaetano Vattemi

Luciano Merlini

Antonella Caputo

Paola Braghetta

Marco Ballestri

P577

2009-02-24T00:00:00Z

http://www.w3.org/2001/XMLSchema#dateTime

P5875

24038149

http://www.w3.org/2001/XMLSchema#string

P698

19240694

http://www.w3.org/2001/XMLSchema#string

P932

2835127

http://www.w3.org/2001/XMLSchema#string