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Q40297453-E01B6E40-4B7F-4137-AF3B-849558F4437F
Q40297453-E01B6E40-4B7F-4137-AF3B-849558F4437F
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Statement
http://www.wikidata.org/entity/statement/Q40297453-E01B6E40-4B7F-4137-AF3B-849558F4437F
AAV gene therapy corrects OTC deficiency and prevents liver fibrosis in aged OTC-knock out heterozygous mice.
P2860
Q40297453-E01B6E40-4B7F-4137-AF3B-849558F4437F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q40297453-E01B6E40-4B7F-4137-AF3B-849558F4437F
rank
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Statement
wasDerivedFrom
777a757c78a39faa731407c962a188e79e9d1aaf
P2860
Preclinical evaluation of a clinical candidate AAV8 vector for ornithine transcarbamylase (OTC) deficiency reveals functional enzyme from each persisting vector genome.