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Q42170619-C36F911D-5036-4B78-8D0B-F9FF5CF9D0F5
Q42170619-C36F911D-5036-4B78-8D0B-F9FF5CF9D0F5
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http://www.wikidata.org/entity/statement/Q42170619-C36F911D-5036-4B78-8D0B-F9FF5CF9D0F5
Optimized human factor IX expression cassettes for hepatic-directed gene therapy of hemophilia B.
P2860
Q42170619-C36F911D-5036-4B78-8D0B-F9FF5CF9D0F5
BestRank
Statement
http://www.wikidata.org/entity/statement/Q42170619-C36F911D-5036-4B78-8D0B-F9FF5CF9D0F5
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type
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wasDerivedFrom
4fce61a4264efe3c5deb8d9ff780fb649cdeb36b
P2860
Preclinical evaluation of a clinical candidate AAV8 vector for ornithine transcarbamylase (OTC) deficiency reveals functional enzyme from each persisting vector genome.