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1
J.YMTHE.2005.11.008
J.YMTHE.2005.11.008
http://dx.doi.org/10.1016/J.YMTHE.2005.11.008
CNS-directed AAV2-mediated gene therapy ameliorates functional deficits in a murine model of infantile neuronal ceroid lipofuscinosis.
P356
Q45889316-BA7C9D80-5F33-4F0E-9C89-8ADEDCC6A201
P356
J.YMTHE.2005.11.008
http://dx.doi.org/10.1016/J.YMTHE.2005.11.008