U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
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Restoration of full-length SMN promoted by adenoviral vectors expressing RNA antisense oligonucleotides embedded in U7 snRNAsInhibition of HIV-1 multiplication by antisense U7 snRNAs and siRNAs targeting cyclophilin AEnhanced exon-skipping induced by U7 snRNA carrying a splicing silencer sequence: Promising tool for DMD therapyU7 snRNAs: a computational surveyDoxycycline-controlled splicing modulation by regulated antisense U7 snRNA expression cassettesBody-wide gene therapy of Duchenne muscular dystrophy in the mdx mouse model.Gene therapy progress and prospects: Duchenne muscular dystrophy.Repair of pre-mRNA splicing: prospects for a therapy for spinal muscular atrophy.The pathogenicity of splicing defects: mechanistic insights into pre-mRNA processing inform novel therapeutic approaches.Nuclear antisense effects in cyclophilin A pre-mRNA splicing by oligonucleotides: a comparison of tricyclo-DNA with LNATranslational research and therapeutic perspectives in dysferlinopathies.The Dynamics of Compound, Transcript, and Protein Effects After Treatment With 2OMePS Antisense Oligonucleotides in mdx Mice.Viral Vector-Mediated Antisense Therapy for Genetic Diseases.In vitro correction of a pseudoexon-generating deep intronic mutation in LGMD2A by antisense oligonucleotides and modified small nuclear RNAs.Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy.AAV genome loss from dystrophic mouse muscles during AAV-U7 snRNA-mediated exon-skipping therapy.The Cellular Processing Capacity Limits the Amounts of Chimeric U7 snRNA Available for Antisense Delivery.Exon skipping and duchenne muscular dystrophy therapy: selection of the most active U1 snRNA antisense able to induce dystrophin exon 51 skipping.Antisense pre-treatment increases gene therapy efficacy in dystrophic muscles.Exon 45 skipping through U1-snRNA antisense molecules recovers the Dys-nNOS pathway and muscle differentiation in human DMD myoblasts.Dystrophin rescue by trans-splicing: a strategy for DMD genotypes not eligible for exon skipping approaches
P2860
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P2860
U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
description
2003 nî lūn-bûn
@nan
2003 թուականի Մարտին հրատարակուած գիտական յօդուած
@hyw
2003 թվականի մարտին հրատարակված գիտական հոդված
@hy
2003年の論文
@ja
2003年論文
@yue
2003年論文
@zh-hant
2003年論文
@zh-hk
2003年論文
@zh-mo
2003年論文
@zh-tw
2003年论文
@wuu
name
U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
@ast
U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
@en
U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
@nl
type
label
U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
@ast
U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
@en
U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
@nl
prefLabel
U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
@ast
U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
@en
U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
@nl
P2093
P356
P1476
U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping
@en
P2093
P2888
P304
P356
10.1007/S000180300047
P407
P577
2003-03-01T00:00:00Z