Randomized, double-blind, placebo-controlled trial of hydroxyurea in spinal muscular atrophy
about
Drug treatment for spinal muscular atrophy types II and IIIDrug treatment for spinal muscular atrophy type IDrug treatment for spinal muscular atrophy types II and IIIDrug treatment for spinal muscular atrophy type ISpinal muscular atrophy: from gene discovery to clinical trialsApplicability of histone deacetylase inhibition for the treatment of spinal muscular atrophySplicing therapy for neuromuscular diseaseEvaluation of SMN protein, transcript, and copy number in the biomarkers for spinal muscular atrophy (BforSMA) clinical studyThe motor neuron response to SMN1 deficiency in spinal muscular atrophyNew therapeutic approaches to spinal muscular atrophy.Therapeutic strategies for the treatment of spinal muscular atrophy.SMN-inducing compounds for the treatment of spinal muscular atrophy.Advances in therapeutic development for spinal muscular atrophy.Treatment of spinal muscular atrophy cells with drugs that upregulate SMN expression reveals inter- and intra-patient variability.Spinal muscular atrophy: journeying from bench to bedsideResistance strength training exercise in children with spinal muscular atrophyTherapy development for spinal muscular atrophy in SMN independent targets.Small Molecules in Development for the Treatment of Spinal Muscular Atrophy.Triptolide increases transcript and protein levels of survival motor neurons in human SMA fibroblasts and improves survival in SMA-like miceA Comparative Study of SMN Protein and mRNA in Blood and Fibroblasts in Patients with Spinal Muscular Atrophy and Healthy ControlsA qualitative study of perceptions of meaningful change in spinal muscular atrophyProspective cohort study of spinal muscular atrophy types 2 and 3.Recent developments in the treatment of Duchenne muscular dystrophy and spinal muscular atrophy.Spinal muscular atrophy: an update on therapeutic progressMouse models of SMA: tools for disease characterization and therapeutic development.Spinal muscular atrophy and the antiapoptotic role of survival of motor neuron (SMN) protein.Neurodegeneration in spinal muscular atrophy: from disease phenotype and animal models to therapeutic strategies and beyond.Strength Testing in Motor Neuron Diseases.Reliability and validity of outcome measures of in-hospital and at-home visits in a randomized, double-blind, placebo-controlled trial for spinal muscular atrophy.Treating pediatric neuromuscular disorders: The future is now.
P2860
Q24200270-71829E20-A162-455B-87F2-F95CE1E9DA26Q24200377-662217E2-437A-476A-BAD2-DF3B93F87C9CQ24234414-C9A8E0FC-AFD6-40D0-97C4-217874B9C335Q24234523-39228917-E2E9-4926-A767-75E904D23CDDQ26824894-20C3248F-052C-449B-90F4-7975312AD2E4Q26864605-EE859660-F65C-4CAB-A3F8-8F7890FA9BD0Q27009581-4ED9CD3F-3EBE-46A5-A861-50D4B85B2941Q28730280-0987C13D-41CA-4D91-97C5-54D8692A8A72Q33874570-9D620057-B727-49EC-9647-965BCDCF59B3Q34237525-A9F0B3B0-BEB9-4BCB-963B-B5F932DB31C3Q34296140-27B1B311-B54A-43B4-9617-7B3AAAA4EF5BQ34312156-C1BBD324-13E0-4819-B711-C35CF4FE0072Q35167319-F9947FA2-8969-4C78-ABB8-679768C0953EQ35304142-90D09117-E95C-4ED4-927C-F3110198BEE9Q35340133-AF5ADFDE-1857-4881-B170-D2BEF98AFBE9Q35864678-18969E4C-F526-41D1-9932-954C4E166B17Q36014761-9048C578-D69B-4B1C-A7EF-5B2B0A1B3FB7Q36095048-44942A86-EFCE-418D-A0C9-0600C778EA9FQ36158983-05A0AB13-20C1-46C4-936D-C3BBB7A6592FQ36205773-4F2F6467-5E57-434A-8179-08D2C94A4A88Q36334820-4DF28A6D-2735-441A-9344-851D6E7AEFBCQ36475291-5267C3A2-8E31-42F7-9F0D-A5E4CBDE1FAEQ36761839-5C527888-2528-45FC-9A00-AC8B3F97402AQ37302832-0EF5C9B1-6CC3-46AF-BEB9-34D71DCADBAFQ38006384-64A949CF-E7EF-41B7-88BE-AC1B08E25E77Q38073714-0DA7D673-1B61-43F7-957F-42589E1DC869Q38197609-8EFC5C1C-4C81-44C5-8823-23B4A2F71531Q38947721-6F83002E-8F11-4D53-8613-56649448D596Q44549555-75872195-AFCB-4E62-A674-C742EB2EBB96Q52756417-14338DE0-18C7-4222-91E5-35BD02D96206
P2860
Randomized, double-blind, placebo-controlled trial of hydroxyurea in spinal muscular atrophy
description
2010 nî lūn-bûn
@nan
2010 թուականի Դեկտեմբերին հրատարակուած գիտական յօդուած
@hyw
2010 թվականի դեկտեմբերին հրատարակված գիտական հոդված
@hy
2010年の論文
@ja
2010年論文
@yue
2010年論文
@zh-hant
2010年論文
@zh-hk
2010年論文
@zh-mo
2010年論文
@zh-tw
2010年论文
@wuu
name
Randomized, double-blind, plac ...... rea in spinal muscular atrophy
@ast
Randomized, double-blind, plac ...... rea in spinal muscular atrophy
@en
Randomized, double-blind, plac ...... rea in spinal muscular atrophy
@nl
type
label
Randomized, double-blind, plac ...... rea in spinal muscular atrophy
@ast
Randomized, double-blind, plac ...... rea in spinal muscular atrophy
@en
Randomized, double-blind, plac ...... rea in spinal muscular atrophy
@nl
prefLabel
Randomized, double-blind, plac ...... rea in spinal muscular atrophy
@ast
Randomized, double-blind, plac ...... rea in spinal muscular atrophy
@en
Randomized, double-blind, plac ...... rea in spinal muscular atrophy
@nl
P2093
P1433
P1476
Randomized, double-blind, plac ...... rea in spinal muscular atrophy
@en
P2093
P304
P356
10.1212/WNL.0B013E3182020332
P407
P577
2010-12-14T00:00:00Z