Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats. - Wikidata - awgldk - TriplyDB

Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats.

Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats.

http://www.wikidata.org/entity/Q30513972

about

Therapies for the bone in mucopolysaccharidoses The effect of neonatal gene therapy on skeletal manifestations in mucopolysaccharidosis VII dogs after a decade.Sensory-motor behavioral characterization of an animal model of Maroteaux-Lamy syndrome (or Mucopolysaccharidosis VI).Therapies of mucopolysaccharidosis IVA (Morquio A syndrome).A review of gene therapy in canine and feline models of lysosomal storage disorders.Whole genome sequencing in cats, identifies new models for blindness in AIPL1 and somite segmentation in HES7.Diagnostic and treatment strategies in mucopolysaccharidosis VI.Neonatal cellular and gene therapies for mucopolysaccharidoses: the earlier the better?The effect of neonatal gene therapy with a gamma retroviral vector on cardiac valve disease in mucopolysaccharidosis VII dogs after a decade Low-dose Gene Therapy Reduces the Frequency of Enzyme Replacement Therapy in a Mouse Model of Lysosomal Storage Disease.Gene delivery strategies for the treatment of mucopolysaccharidoses.Emerging drugs for the treatment of mucopolysaccharidoses.

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P2860

Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats.

http://www.wikidata.org/entity/Q30513972

description

2012 nî lūn-bûn

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2012 թուականի Մարտին հրատարակուած գիտական յօդուած

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2012 թվականի մարտին հրատարակված գիտական հոդված

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2012年の論文

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2012年論文

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2012年論文

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2012年論文

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2012年論文

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2012年論文

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2012年论文

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name

Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats.

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Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats.

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type

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Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats.

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Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats.

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Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats.

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Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats.

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Molecular Therapy

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Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats

@en

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Anne M Traas

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Bin Wang

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Emma J Parkinson-Lawrence

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Jason A Metcalf

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John J Hopwood

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Katherine P Ponder

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Mark E Haskins

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Meg M Sleeper

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N Matthew Ellinwood

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Patricia A O'Donnell

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P2860

Gene therapy for mucopolysaccharidosis

SUMF1 enhances sulfatase activities in vivo in five sulfatase deficiencies

Early neurodegeneration progresses independently of microglial activation by heparan sulfate in the brain of mucopolysaccharidosis IIIB mice

Multiple sulfatase deficiency is caused by mutations in the gene encoding the human C(alpha)-formylglycine generating enzyme

The multiple sulfatase deficiency gene encodes an essential and limiting factor for the activity of sulfatases

Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs.

A self-inactivating gamma-retroviral vector reduces manifestations of mucopolysaccharidosis I in mice

Long-term amelioration of feline Mucopolysaccharidosis VI after AAV-mediated liver gene transfer

Radiographic evaluation of bones and joints in mucopolysaccharidosis I and VII dogs after neonatal gene therapy.

Involvement of the Toll-like receptor 4 pathway and use of TNF-alpha antagonists for treatment of the mucopolysaccharidoses

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898-907

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scholarly article

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10.1038/MT.2012.9

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5

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20

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Gustavo D Aguirre

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2012-03-06T00:00:00Z

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22395531

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