Pharmacokinetics, safety and tolerability of miglustat in the treatment of pediatric patients with GM2 gangliosidosis.
about
Developing therapeutic approaches for metachromatic leukodystrophyThe development and use of small molecule inhibitors of glycosphingolipid metabolism for lysosomal storage diseases.Corneal alterations during combined therapy with cyclodextrin/allopregnanolone and miglustat in a knock-out mouse model of NPC1 disease.Emerging therapies for neurodegenerative lysosomal storage disorders - from concept to reality.Infantile gangliosidoses: Mapping a timeline of clinical changes.Scalable syntheses of both enantiomers of DNJNAc and DGJNAc from glucuronolactone: the effect of N-alkylation on hexosaminidase inhibition.Miglustat therapy in juvenile Sandhoff disease.Substrate deprivation therapy in juvenile Sandhoff disease.Lipidomic profiling links the Fanconi anemia pathway to glycosphingolipid metabolism in head and neck cancer cells.
P2860
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P2860
Pharmacokinetics, safety and tolerability of miglustat in the treatment of pediatric patients with GM2 gangliosidosis.
description
2009 nî lūn-bûn
@nan
2009 թուականի Մայիսին հրատարակուած գիտական յօդուած
@hyw
2009 թվականի մայիսին հրատարակված գիտական հոդված
@hy
2009年の論文
@ja
2009年論文
@yue
2009年論文
@zh-hant
2009年論文
@zh-hk
2009年論文
@zh-mo
2009年論文
@zh-tw
2009年论文
@wuu
name
Pharmacokinetics, safety and t ...... ients with GM2 gangliosidosis.
@ast
Pharmacokinetics, safety and t ...... ients with GM2 gangliosidosis.
@en
type
label
Pharmacokinetics, safety and t ...... ients with GM2 gangliosidosis.
@ast
Pharmacokinetics, safety and t ...... ients with GM2 gangliosidosis.
@en
prefLabel
Pharmacokinetics, safety and t ...... ients with GM2 gangliosidosis.
@ast
Pharmacokinetics, safety and t ...... ients with GM2 gangliosidosis.
@en
P2093
P1476
Pharmacokinetics, safety and t ...... ients with GM2 gangliosidosis.
@en
P2093
Brenda Banwell
Christopher P Morgan
Cynthia J Tifft
Jasper Dingemanse
Joe T R Clarke
Paul L M van Giersbergen
Sandra Yang
P304
P356
10.1016/J.YMGME.2009.04.013
P577
2009-05-03T00:00:00Z