Patient-reported outcomes in clinical trials of rare diseases.

Patient-reported outcomes in clinical trials of rare diseases.

Item
http://www.wikidata.org/entity/Q34011926
Symptom burden and life challenges reported by adult chordoma patients and their caregivers.Concept-elicitation phase for the development of the pediatric patient-reported outcome version of the Common Terminology Criteria for Adverse Events.Establishing core outcome sets for phenylketonuria (PKU) and medium-chain Acyl-CoA dehydrogenase (MCAD) deficiency in children: study protocol for systematic reviews and Delphi surveys.Provincial development of a patient-reported outcome initiative to guide patient care, quality improvement, and research.Patient reported outcome measures in rare diseases: a narrative review.Multicentre cross-sectional clinical evaluation study about quality of life in adults with disorders/differences of sex development (DSD) compared to country specific reference populations (dsd-LIFE).Low rates of patient-reported outcome claims for orphan drugs approved by the us food and drug administration.Using a meta-narrative literature review and focus groups with key stakeholders to identify perceived challenges and solutions for generating robust evidence on the effectiveness of treatments for rare diseases.Patient-reported outcome claims in European and United States orphan drug approvals
P2860

Patient-reported outcomes in clinical trials of rare diseases.

Item
http://www.wikidata.org/entity/Q34011926
description
2014 nî lūn-bûn
@nan
2014 թուականի Օգոստոսին հրատարակուած գիտական յօդուած
@hyw
2014 թվականի օգոստոսին հրատարակված գիտական հոդված
@hy
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
name
Patient-reported outcomes in clinical trials of rare diseases.
@ast
Patient-reported outcomes in clinical trials of rare diseases.
@en
Patient-reported outcomes in clinical trials of rare diseases.
@nl
type
label
Patient-reported outcomes in clinical trials of rare diseases.
@ast
Patient-reported outcomes in clinical trials of rare diseases.
@en
Patient-reported outcomes in clinical trials of rare diseases.
@nl
prefLabel
Patient-reported outcomes in clinical trials of rare diseases.
@ast
Patient-reported outcomes in clinical trials of rare diseases.
@en
Patient-reported outcomes in clinical trials of rare diseases.
@nl
P1433
P1476
P2093
P2860
P2888
P304
P31
P356
P478
P50
P577
P5875
P6179
P698
P921
P932
P356
P1433
P1476
Patient-reported outcomes in clinical trials of rare diseases.
@en
P2093
P2860
P2888
P304
P31
P356
P478
P50
P577
P5875
P6179
P698
P921
P932