Adeno-associated virus-mediated correction of a canine model of glycogen storage disease type Ia.
about
Glucose-6-phosphatase deficiencyLong-term efficacy following readministration of an adeno-associated virus vector in dogs with glycogen storage disease type IaGlycogen storage disease type Ia in canines: a model for human metabolic and genetic liver diseaseEnhanced efficacy from gene therapy in Pompe disease using coreceptor blockadeRecombinant AAV-directed gene therapy for type I glycogen storage diseases.Perinatal gene transfer to the liver.AAV8-mediated hepatic gene transfer in infant rhesus monkeys (Macaca mulatta)Preclinical Development of New Therapy for Glycogen Storage Diseases.Large animal models and new therapies for glycogen storage disease.Hepatic gene transfer in neonatal mice by adeno-associated virus serotype 8 vector.In Vivo Zinc Finger Nuclease-mediated Targeted Integration of a Glucose-6-phosphatase Transgene Promotes Survival in Mice With Glycogen Storage Disease Type IA.Pathogenesis of growth failure and partial reversal with gene therapy in murine and canine Glycogen Storage Disease type IaRecombinant adeno-associated virus vectors in the treatment of rare diseases.The function of dog models in developing gene therapy strategies for human health.Type I glycogen storage diseases: disorders of the glucose-6-phosphatase/glucose-6-phosphate transporter complexes.Diagnosis and management of glycogen storage disease type I: a practice guideline of the American College of Medical Genetics and Genomics.The liver as a target organ for gene therapy: state of the art, challenges, and future perspectives.Repeated AAV-mediated gene transfer by serotype switching enables long-lasting therapeutic levels of hUgt1a1 enzyme in a mouse model of Crigler-Najjar Syndrome Type I.Gene Therapy in Tyrosinemia: Potential and Pitfalls.Immunological ignorance allows long-term gene expression after perinatal recombinant adeno-associated virus-mediated gene transfer to murine airways.Rescue administration of a helper-dependent adenovirus vector with long-term efficacy in dogs with glycogen storage disease type Ia.In search of proof-of-concept: gene therapy for glycogen storage disease type Ia.G6PC mRNA Therapy Positively Regulates Fasting Blood Glucose and Decreases Liver Abnormalities in a Mouse Model of Glycogen Storage Disease 1a.
P2860
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P2860
Adeno-associated virus-mediated correction of a canine model of glycogen storage disease type Ia.
description
2010 nî lūn-bûn
@nan
2010 թուականի Յուլիսին հրատարակուած գիտական յօդուած
@hyw
2010 թվականի հուլիսին հրատարակված գիտական հոդված
@hy
2010年の論文
@ja
2010年論文
@yue
2010年論文
@zh-hant
2010年論文
@zh-hk
2010年論文
@zh-mo
2010年論文
@zh-tw
2010年论文
@wuu
name
Adeno-associated virus-mediate ...... cogen storage disease type Ia.
@ast
Adeno-associated virus-mediate ...... cogen storage disease type Ia.
@en
Adeno-associated virus-mediate ...... cogen storage disease type Ia.
@nl
type
label
Adeno-associated virus-mediate ...... cogen storage disease type Ia.
@ast
Adeno-associated virus-mediate ...... cogen storage disease type Ia.
@en
Adeno-associated virus-mediate ...... cogen storage disease type Ia.
@nl
prefLabel
Adeno-associated virus-mediate ...... cogen storage disease type Ia.
@ast
Adeno-associated virus-mediate ...... cogen storage disease type Ia.
@en
Adeno-associated virus-mediate ...... cogen storage disease type Ia.
@nl
P2093
P2860
P356
P1433
P1476
Adeno-associated virus-mediate ...... cogen storage disease type Ia.
@en
P2093
Andrew Specht
Barry J Byrne
Catherine E Correia
Cathryn S Mah
Darin J Falk
David A Weinstein
Gurmeet Dhaliwal
Harvey E Ramirez
Holly Cossette
Janice Y Chou
P2860
P304
P356
10.1089/HUM.2009.157
P577
2010-07-01T00:00:00Z