Hematopoietic stem cell transplantation and hematopoietic stem cell gene therapy in X-linked adrenoleukodystrophy.
about
Current and future pharmacological treatment strategies in X-linked adrenoleukodystrophyPeroxisomes in brain development and functionCloning humans? Biological, ethical, and social considerationsThe genetic landscape of X-linked adrenoleukodystrophy: inheritance, mutations, modifier genes, and diagnosisBone marrow cell recruitment to the brain in the absence of irradiation or parabiosis biasThe role of microglia in human disease: therapeutic tool or target?Abcd2 is a strong modifier of the metabolic impairments in peritoneal macrophages of ABCD1-deficient miceViral and nonviral delivery systems for gene deliveryPathophysiology of X-linked adrenoleukodystrophy.Arrayed lentiviral barcoding for quantification analysis of hematopoietic dynamics.X-linked adrenoleukodystrophy: correlation between Loes score and diffusion tensor imaging parameters.Exome sequencing identifies mutations in ABCD1 and DACH2 in two brothers with a distinct phenotype.Evaluation of retinoids for induction of the redundant gene ABCD2 as an alternative treatment option in X-linked adrenoleukodystrophy.Retroviral vectors: post entry events and genomic alterations.Functional genomic analysis unravels a metabolic-inflammatory interplay in adrenoleukodystrophyClinical utility gene card for: adrenoleukodystrophy.Activation of sirtuin 1 as therapy for the peroxisomal disease adrenoleukodystrophy.Progress in gene therapy for prostate cancerVpx mediated degradation of SAMHD1 has only a very limited effect on lentiviral transduction rate in ex vivo cultured HSPCs.Clinical reasoning: a 56-year-old man with progressive spasticityClinical manifest x-linked recessive adrenoleukodystrophy in a female.Childhood Cerebral Adrenoleukodystrophy: MR Perfusion Measurements and Their Use in Predicting Clinical Outcome after Hematopoietic Stem Cell Transplantation.Newborn screening for lysosomal storage disorders and other neuronopathic conditions.Newborn screening for X-linked adrenoleukodystrophy: further evidence high throughput screening is feasible.Inborn errors of metabolism causing epilepsy.Advances and pitfalls of cell therapy in metabolic leukodystrophies.Recent gene therapy advancements for neurological diseases.A Thyroid Hormone-Based Strategy for Correcting the Biochemical Abnormality in X-Linked Adrenoleukodystrophy.Viral vectors for therapy of neurologic diseases.X-linked adrenoleukodystrophy: very long-chain fatty acid metabolism is severely impaired in monocytes but not in lymphocytes.Phenotypic variability in a family with x-linked adrenoleukodystrophy caused by the p.Trp132Ter mutation.Gene Delivery Approaches for Mesenchymal Stem Cell Therapy: Strategies to Increase Efficiency and Specificity.Superior long-term repopulating capacity of G-CSF+plerixafor-mobilized blood: implications for stem cell gene therapy by studies in the Hbb(th-3) mouse model.Introducing PeptoPlexes: polylysine-block-polysarcosine based polyplexes for transfection of HEK 293T cells.Healing genes in the nervous system.Hematopoietic Stem Cell Gene Therapy: Progress and Lessons Learned.Lipid homeostasis and inflammatory activation are disturbed in classically activated macrophages with peroxisomal β-oxidation deficiency.Do circulating cells transdifferentiate and replenish stem cell pools in the brain and periphery?Identification of a chronic non-neurodegenerative microglia activation state in a mouse model of peroxisomal β-oxidation deficiency.Toward a better understanding of brain lesions during metachromatic leukodystrophy evolution.
P2860
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P2860
Hematopoietic stem cell transplantation and hematopoietic stem cell gene therapy in X-linked adrenoleukodystrophy.
description
2010 nî lūn-bûn
@nan
2010 թուականի Յուլիսին հրատարակուած գիտական յօդուած
@hyw
2010 թվականի հուլիսին հրատարակված գիտական հոդված
@hy
2010年の論文
@ja
2010年論文
@yue
2010年論文
@zh-hant
2010年論文
@zh-hk
2010年論文
@zh-mo
2010年論文
@zh-tw
2010年论文
@wuu
name
Hematopoietic stem cell transp ...... X-linked adrenoleukodystrophy.
@ast
Hematopoietic stem cell transp ...... X-linked adrenoleukodystrophy.
@en
Hematopoietic stem cell transp ...... X-linked adrenoleukodystrophy.
@nl
type
label
Hematopoietic stem cell transp ...... X-linked adrenoleukodystrophy.
@ast
Hematopoietic stem cell transp ...... X-linked adrenoleukodystrophy.
@en
Hematopoietic stem cell transp ...... X-linked adrenoleukodystrophy.
@nl
prefLabel
Hematopoietic stem cell transp ...... X-linked adrenoleukodystrophy.
@ast
Hematopoietic stem cell transp ...... X-linked adrenoleukodystrophy.
@en
Hematopoietic stem cell transp ...... X-linked adrenoleukodystrophy.
@nl
P1433
P1476
Hematopoietic stem cell transp ...... X-linked adrenoleukodystrophy.
@en
P2093
Nathalie Cartier
Patrick Aubourg
P304
P356
10.1111/J.1750-3639.2010.00394.X
P577
2010-07-01T00:00:00Z