New strategies for enzyme replacement therapy for lysosomal storage diseases
about
Therapeutic efficacy of nanomedicines for prostate cancer: An updateUtilization of Glycosaminoglycans/Proteoglycans as Carriers for Targeted Therapy DeliveryOrganelle targeting: third level of drug targetingNewborn screening and diagnosis of mucopolysaccharidosesEnzyme replacement therapy attenuates disease progression in a canine model of late-infantile neuronal ceroid lipofuscinosis (CLN2 disease).β2 Agonists enhance the efficacy of simultaneous enzyme replacement therapy in murine Pompe disease.Long circulating enzyme replacement therapy rescues bone pathology in mucopolysaccharidosis VII murine model.Adjunctive β2-agonists reverse neuromuscular involvement in murine Pompe disease.The final frontier -- crossing the blood-brain barrier.Insulin-like growth factor II peptide fusion enables uptake and lysosomal delivery of α-N-acetylglucosaminidase to mucopolysaccharidosis type IIIB fibroblasts.A peptide-linked recombinant glucocerebrosidase for targeted neuronal delivery: Design, production, and assessment.Blood-brain barrier structure and function and the challenges for CNS drug delivery.Insulin-Like Growth Factor-II/Cation-Independent Mannose 6-Phosphate Receptor in Neurodegenerative Diseases.Mannose-6-phosphate receptor: a target for theranostics of prostate cancer.HIV Tat Domain Improves Cross-correction of Human Galactocerebrosidase in a Gene- and Flanking Sequence-dependent Manner.Bidirectional apical-basal traffic of the cation-independent mannose-6-phosphate receptor in brain endothelial cells.Selective plasma pharmacokinetics and brain uptake in the mouse of enzyme fusion proteins derived from species-specific receptor-targeted antibodies.α-Galactosidase-A Loaded-Nanoliposomes with Enhanced Enzymatic Activity and Intracellular Penetration.Delivery of Cargo to Lysosomes Using GNeosomes.Fast, sensitive method for trisaccharide biomarker detection in mucopolysaccharidosis type 1.
P2860
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P2860
New strategies for enzyme replacement therapy for lysosomal storage diseases
description
2010 nî lūn-bûn
@nan
2010 թուականի Ապրիլին հրատարակուած գիտական յօդուած
@hyw
2010 թվականի ապրիլին հրատարակված գիտական հոդված
@hy
2010年の論文
@ja
2010年論文
@yue
2010年論文
@zh-hant
2010年論文
@zh-hk
2010年論文
@zh-mo
2010年論文
@zh-tw
2010年论文
@wuu
name
New strategies for enzyme replacement therapy for lysosomal storage diseases
@ast
New strategies for enzyme replacement therapy for lysosomal storage diseases
@en
New strategies for enzyme replacement therapy for lysosomal storage diseases
@nl
type
label
New strategies for enzyme replacement therapy for lysosomal storage diseases
@ast
New strategies for enzyme replacement therapy for lysosomal storage diseases
@en
New strategies for enzyme replacement therapy for lysosomal storage diseases
@nl
prefLabel
New strategies for enzyme replacement therapy for lysosomal storage diseases
@ast
New strategies for enzyme replacement therapy for lysosomal storage diseases
@en
New strategies for enzyme replacement therapy for lysosomal storage diseases
@nl
P2093
P2860
P356
P1476
New strategies for enzyme replacement therapy for lysosomal storage diseases
@en
P2093
Carole Vogler
Jeffrey H Grubb
William S Sly
P2860
P304
P356
10.1089/REJ.2009.0920
P407
P577
2010-04-01T00:00:00Z