Liver-directed gene therapy corrects cardiovascular lesions in feline mucopolysaccharidosis type I
about
Companion animals: Translational scientist's new best friendsAortic Root Dilatation in Mucopolysaccharidosis I-VIIIn Vivo NMR Studies of the Brain with Hereditary or Acquired Metabolic Disorders.A review of gene therapy in canine and feline models of lysosomal storage disorders.Neonatal Systemic AAV Induces Tolerance to CNS Gene Therapy in MPS I Dogs and Nonhuman Primates.Recombinant adeno-associated virus vectors in the treatment of rare diseases.The Carotid Intima-Media Thickness and Arterial Stiffness of Pediatric Mucopolysaccharidosis Patients Are Increased Compared to Both Pediatric and Adult ControlsRecent advances in gene therapy for lysosomal storage disorders.Adeno-Associated Virus-Based Gene Therapy for CNS Diseases.Gene therapy for lysosomal storage disorders: recent advances for metachromatic leukodystrophy and mucopolysaccaridosis I.Intranasal Adeno-Associated Virus Mediated Gene Delivery and Expression of Human Iduronidase in the Central Nervous System: A Noninvasive and Effective Approach for Prevention of Neurologic Disease in Mucopolysaccharidosis Type I.Transient suppression of hepatocellular replication in the mouse liver following transduction with recombinant adeno-associated virus.
P2860
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P2860
Liver-directed gene therapy corrects cardiovascular lesions in feline mucopolysaccharidosis type I
description
2014 nî lūn-bûn
@nan
2014 թուականի Սեպտեմբերին հրատարակուած գիտական յօդուած
@hyw
2014 թվականի սեպտեմբերին հրատարակված գիտական հոդված
@hy
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
name
Liver-directed gene therapy co ...... e mucopolysaccharidosis type I
@ast
Liver-directed gene therapy co ...... e mucopolysaccharidosis type I
@en
Liver-directed gene therapy co ...... e mucopolysaccharidosis type I
@nl
type
label
Liver-directed gene therapy co ...... e mucopolysaccharidosis type I
@ast
Liver-directed gene therapy co ...... e mucopolysaccharidosis type I
@en
Liver-directed gene therapy co ...... e mucopolysaccharidosis type I
@nl
prefLabel
Liver-directed gene therapy co ...... e mucopolysaccharidosis type I
@ast
Liver-directed gene therapy co ...... e mucopolysaccharidosis type I
@en
Liver-directed gene therapy co ...... e mucopolysaccharidosis type I
@nl
P2093
P2860
P356
P1476
Liver-directed gene therapy co ...... e mucopolysaccharidosis type I
@en
P2093
Christian Hinderer
Jean-Pierre Louboutin
Jessica Bagel
Mark E Haskins
Patricia O'Donnell
Peter Bell
Qiang Wang
Therese Ruane
Tracey Sikora
P2860
P304
14894-14899
P356
10.1073/PNAS.1413645111
P407
P577
2014-09-29T00:00:00Z