Broad therapeutic benefit after RNAi expression vector delivery to deep cerebellar nuclei: implications for spinocerebellar ataxia type 1 therapy
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Gene, Stem Cell, and Alternative Therapies for SCA 1Precision medicine in spinocerebellar ataxias: treatment based on common mechanisms of diseaseBroad distribution of ataxin 1 silencing in rhesus cerebella for spinocerebellar ataxia type 1 therapy.Gene suppression strategies for dominantly inherited neurodegenerative diseases: lessons from Huntington's disease and spinocerebellar ataxia.Single nucleotide seed modification restores in vivo tolerability of a toxic artificial miRNA sequence in the mouse brain.Assessing recovery from neurodegeneration in spinocerebellar ataxia 1: Comparison of in vivo magnetic resonance spectroscopy with motor testing, gene expression and histology.RNA interference-based therapy for spinocerebellar ataxia type 7 retinal degeneration.Gene therapy for the nervous system: challenges and new strategies.Nonallele specific silencing of ataxin-7 improves disease phenotypes in a mouse model of SCA7.RNAi prevents and reverses phenotypes induced by mutant human ataxin-1.RNA Interference of Human α-Synuclein in Mouse.Targeted Molecular Therapies for SBMA.MR-guided parenchymal delivery of adeno-associated viral vector serotype 5 in non-human primate brain.New developments in RAN translation: insights from multiple diseases.RpA1 ameliorates symptoms of mutant ataxin-1 knock-in mice and enhances DNA damage repair.Neuronal Atrophy Early in Degenerative Ataxia Is a Compensatory Mechanism to Regulate Membrane Excitability.Antisense oligonucleotide therapy for spinocerebellar ataxia type 2.Epigenetic profiles in polyglutamine disorders.Oligonucleotide therapeutics in neurodegenerative diseases.Reduction of protein kinase A-mediated phosphorylation of ATXN1-S776 in Purkinje cells delays onset of Ataxia in a SCA1 mouse model.
P2860
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P2860
Broad therapeutic benefit after RNAi expression vector delivery to deep cerebellar nuclei: implications for spinocerebellar ataxia type 1 therapy
description
2013 nî lūn-bûn
@nan
2013 թուականի Դեկտեմբերին հրատարակուած գիտական յօդուած
@hyw
2013 թվականի դեկտեմբերին հրատարակված գիտական հոդված
@hy
2013年の論文
@ja
2013年論文
@yue
2013年論文
@zh-hant
2013年論文
@zh-hk
2013年論文
@zh-mo
2013年論文
@zh-tw
2013年论文
@wuu
name
Broad therapeutic benefit afte ...... rebellar ataxia type 1 therapy
@ast
Broad therapeutic benefit afte ...... rebellar ataxia type 1 therapy
@en
Broad therapeutic benefit afte ...... rebellar ataxia type 1 therapy
@nl
type
label
Broad therapeutic benefit afte ...... rebellar ataxia type 1 therapy
@ast
Broad therapeutic benefit afte ...... rebellar ataxia type 1 therapy
@en
Broad therapeutic benefit afte ...... rebellar ataxia type 1 therapy
@nl
prefLabel
Broad therapeutic benefit afte ...... rebellar ataxia type 1 therapy
@ast
Broad therapeutic benefit afte ...... rebellar ataxia type 1 therapy
@en
Broad therapeutic benefit afte ...... rebellar ataxia type 1 therapy
@nl
P2860
P356
P1433
P1476
Broad therapeutic benefit afte ...... rebellar ataxia type 1 therapy
@en
P2093
Beverly L Davidson
Megan S Keiser
P2860
P304
P356
10.1038/MT.2013.279
P577
2013-12-12T00:00:00Z