A sensitive assay system to test antisense oligonucleotides for splice suppression therapy in the mouse liver.
about
Delivery is key: lessons learnt from developing splice-switching antisense therapiesCorrecting the NLRP3 inflammasome deficiency in macrophages from autoimmune NZB mice with exon skipping antisense oligonucleotides.Intronic PAH gene mutations cause a splicing defect by a novel mechanism involving U1snRNP binding downstream of the 5' splice site.
P2860
A sensitive assay system to test antisense oligonucleotides for splice suppression therapy in the mouse liver.
description
2014 nî lūn-bûn
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2014 թուականի Սեպտեմբերին հրատարակուած գիտական յօդուած
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2014 թվականի սեպտեմբերին հրատարակված գիտական հոդված
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2014年の論文
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2014年学术文章
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2014年学术文章
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2014年学术文章
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2014年学术文章
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2014年學術文章
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name
A sensitive assay system to te ...... on therapy in the mouse liver.
@ast
A sensitive assay system to te ...... on therapy in the mouse liver.
@en
A sensitive assay system to te ...... on therapy in the mouse liver.
@nl
type
label
A sensitive assay system to te ...... on therapy in the mouse liver.
@ast
A sensitive assay system to te ...... on therapy in the mouse liver.
@en
A sensitive assay system to te ...... on therapy in the mouse liver.
@nl
prefLabel
A sensitive assay system to te ...... on therapy in the mouse liver.
@ast
A sensitive assay system to te ...... on therapy in the mouse liver.
@en
A sensitive assay system to te ...... on therapy in the mouse liver.
@nl
P2093
P2860
P356
P1476
A sensitive assay system to te ...... ion therapy in the mouse liver
@en
P2093
Beat Thöny
Belén Pérez
Cary O Harding
Hiu Man Viecelli
Lourdes R Desviat
Magdalena Ugarte
P2860
P356
10.1038/MTNA.2014.44
P577
2014-09-16T00:00:00Z