Gene therapy for lysosomal storage disorders: a good start.
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Impact of lysosome status on extracellular vesicle content and releaseLow-dose Gene Therapy Reduces the Frequency of Enzyme Replacement Therapy in a Mouse Model of Lysosomal Storage Disease.Biomarkers in Lysosomal Storage DiseasesPresentation and Treatments for Mucopolysaccharidosis Type II (MPS II; Hunter Syndrome).Cryo-EM structures of the human endolysosomal TRPML3 channel in three distinct states.Human iPSC-based models highlight defective glial and neuronal differentiation from neural progenitor cells in metachromatic leukodystrophy.
P2860
Gene therapy for lysosomal storage disorders: a good start.
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2015 nî lūn-bûn
@nan
2015 թուականի Նոյեմբերին հրատարակուած գիտական յօդուած
@hyw
2015 թվականի նոյեմբերին հրատարակված գիտական հոդված
@hy
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
name
Gene therapy for lysosomal storage disorders: a good start.
@ast
Gene therapy for lysosomal storage disorders: a good start.
@en
Gene therapy for lysosomal storage disorders: a good start.
@nl
type
label
Gene therapy for lysosomal storage disorders: a good start.
@ast
Gene therapy for lysosomal storage disorders: a good start.
@en
Gene therapy for lysosomal storage disorders: a good start.
@nl
prefLabel
Gene therapy for lysosomal storage disorders: a good start.
@ast
Gene therapy for lysosomal storage disorders: a good start.
@en
Gene therapy for lysosomal storage disorders: a good start.
@nl
P2860
P356
P1476
Gene therapy for lysosomal storage disorders: a good start.
@en
P2093
Alessandra Biffi
P2860
P304
P356
10.1093/HMG/DDV457
P577
2015-11-24T00:00:00Z