Dystromirs as serum biomarkers for monitoring the disease severity in Duchenne muscular Dystrophy.
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Clinical utility of serum biomarkers in Duchenne muscular dystrophyNoncoding RNAs, Emerging Regulators of Skeletal Muscle Development and DiseasesTranscriptome Analysis of Ullrich Congenital Muscular Dystrophy Fibroblasts Reveals a Disease Extracellular Matrix Signature and Key Molecular RegulatorsSelective release of muscle-specific, extracellular microRNAs during myogenic differentiationMega roles of microRNAs in regulation of skeletal muscle health and diseaseCirculating Muscle-specific miRNAs in Duchenne Muscular Dystrophy PatientsDiscovery of serum protein biomarkers in the mdx mouse model and cross-species comparison to Duchenne muscular dystrophy patients.MiR-206, a key modulator of skeletal muscle development and disease.Serum creatinine level: a supplemental index to distinguish Duchenne muscular dystrophy from Becker muscular dystrophy.How much dystrophin is enough: the physiological consequences of different levels of dystrophin in the mdx mouseSix Serum miRNAs Fail to Validate as Myotonic Dystrophy Type 1 Biomarkers.Discovery of Metabolic Biomarkers for Duchenne Muscular Dystrophy within a Natural History Study.Identification in GRMD dog muscle of critical miRNAs involved in pathophysiology and effects associated with MuStem cell transplantation.Skeletal Muscle MicroRNAs: Their Diagnostic and Therapeutic Potential in Human Muscle Diseases.Serum Levels of MicroRNA-206 and Novel Mini-STR Assays for Carrier Detection in Duchenne Muscular Dystrophy.Altered Levels of MicroRNA-9, -206, and -132 in Spinal Muscular Atrophy and Their Response to Antisense Oligonucleotide TherapyValidation of plasma microRNAs as biomarkers for myotonic dystrophy type 1.Establishment of a highly sensitive sandwich ELISA for the N-terminal fragment of titin in urineCirculating Biomarkers for Duchenne Muscular Dystrophy.Muscle-Derived Proteins as Serum Biomarkers for Monitoring Disease Progression in Three Forms of Muscular Dystrophy.Drug Discovery of Therapies for Duchenne Muscular Dystrophy.Extracellular microRNAs in Membrane Vesicles and Non-vesicular Carriers.Eteplirsen: First Global Approval.Micro-RNA expression in muscle and fiber morphometry in myotonic dystrophy type 1.Reduced serum myostatin concentrations associated with genetic muscle disease progression.MicroRNA and mRNA Expression Changes in Steroid Naïve and Steroid Treated DMD Patients.Decreased myoblast differentiation in chronic binge alcohol-administered simian immunodeficiency virus-infected male macaques: role of decreased miR-206.Micro-RNAs in ALS muscle: Differences in gender, age at onset and disease duration.N-terminal α Dystroglycan (αDG-N): A Potential Serum Biomarker for Duchenne Muscular Dystrophy.Circulating miRNAs are generic and versatile therapeutic monitoring biomarkers in muscular dystrophies.Neo-epitope Peptides as Biomarkers of Disease Progression for Muscular Dystrophies and Other Myopathies.MRC Centre Neuromuscular Biobank (Newcastle and London): Supporting and facilitating rare and neuromuscular disease research worldwide.Duchenne and Becker Muscular Dystrophies: A Review of Animal Models, Clinical End Points, and Biomarker Quantification.226th ENMC International Workshop:: Towards validated and qualified biomarkers for therapy development for Duchenne muscular dystrophy 20-22 January 2017, Heemskerk, The Netherlands.Circulating myomiRs: a new class of biomarkers to monitor skeletal muscle in physiology and medicine.Noncoding RNAs and Duchenne muscular dystrophy.Muscle-specific microRNA-206 targets multiple components in dystrophic skeletal muscle representing beneficial adaptations.Influence of physical exercise on microRNAs in skeletal muscle regeneration, aging and diseases.Examining the Genetic Background of Porcine Muscle Growth and Development Based on Transcriptome and miRNAome Data.Eteplirsen.
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P2860
Dystromirs as serum biomarkers for monitoring the disease severity in Duchenne muscular Dystrophy.
description
2013 nî lūn-bûn
@nan
2013 թուականի Նոյեմբերին հրատարակուած գիտական յօդուած
@hyw
2013 թվականի նոյեմբերին հրատարակված գիտական հոդված
@hy
2013年の論文
@ja
2013年論文
@yue
2013年論文
@zh-hant
2013年論文
@zh-hk
2013年論文
@zh-mo
2013年論文
@zh-tw
2013年论文
@wuu
name
Dystromirs as serum biomarkers ...... n Duchenne muscular Dystrophy.
@ast
Dystromirs as serum biomarkers ...... n Duchenne muscular Dystrophy.
@en
type
label
Dystromirs as serum biomarkers ...... n Duchenne muscular Dystrophy.
@ast
Dystromirs as serum biomarkers ...... n Duchenne muscular Dystrophy.
@en
prefLabel
Dystromirs as serum biomarkers ...... n Duchenne muscular Dystrophy.
@ast
Dystromirs as serum biomarkers ...... n Duchenne muscular Dystrophy.
@en
P2093
P2860
P50
P1433
P1476
Dystromirs as serum biomarkers ...... n Duchenne muscular Dystrophy.
@en
P2093
Alessandra Ferlini
Francesco Muntoni
Irina T Zaharieva
James Collins
Jennifer E Morgan
Kate Bushby
Mariacristina Scoto
Mattia Calissano
Michela Guglieri
P2860
P304
P356
10.1371/JOURNAL.PONE.0080263
P407
P577
2013-11-25T00:00:00Z