about
Customizing the genome as therapy for the β-hemoglobinopathiesThe Rise of CRISPR/Cas for Genome Editing in Stem CellsGenome Editing and Its Applications in Model OrganismsCRISPR/Cas9-Mediated Correction of the FANCD1 Gene in Primary Patient CellsApplications of CRISPR technologies in research and beyond.Gene editing toward the use of autologous therapies in recessive dystrophic epidermolysis bullosa.The Simple Chordate Ciona intestinalis Has a Reduced Complement of Genes Associated with Fanconi Anemia.The CRISPR/Cas9 System and the Possibility of Genomic Edition for CardiologyConcise Review: Getting to the Core of Inherited Bone Marrow Failures.Sequence-specific DNA nicking endonucleases.Modeling Disease In Vivo With CRISPR/Cas9.Developmental history and application of CRISPR in human disease.CRISPR-Cas orthologues and variants: optimizing the repertoire, specificity and delivery of genome engineering tools.To CRISPR and beyond: the evolution of genome editing in stem cells.CRISPR-Cas9 technology and its application in haematological disorders.Gene editing and its application for hematological diseases.Modeling craniofacial and skeletal congenital birth defects to advance therapies.Emerging cellular and gene therapies for congenital anemias.CRISPR-Based Technologies for the Manipulation of Eukaryotic Genomes.Hematopoietic cell transplantation in Fanconi anemia: current evidence, challenges and recommendations.Therapeutic gene editing: delivery and regulatory perspectivesCRISPR/Cas9 Targeted Gene Editing and Cellular Engineering in Fanconi Anemia.Stem Cell Therapy for Fanconi Anemia.Viral Vectors, Engineered Cells and the CRISPR Revolution.Addressing challenges in the clinical applications associated with CRISPR/Cas9 technology and ethical questions to prevent its misuse.The Future of CRISPR Applications in the Lab, the Clinic and Society.Human genetic variation alters CRISPR-Cas9 on- and off-targeting specificity at therapeutically implicated loci.CRISPR/Cas9-based genetic correction for recessive dystrophic epidermolysis bullosa.Bloom syndrome: research and data priorities for the development of precision medicine as identified by some affected families.Ex Vivo COL7A1 Correction for Recessive Dystrophic Epidermolysis Bullosa Using CRISPR/Cas9 and Homology-Directed RepairTargeted genome editing in acute lymphoblastic leukemia: a reviewPerspectives on gene therapy for Fanconi anemia
P2860
Q26751061-D2BF79A3-7782-4013-ACB9-0CA0FAB2BD90Q26765852-0E155D35-4F73-4C94-B333-1135DF79F7A3Q26772108-DFDC4E7D-9B09-4612-862D-D440CC7806AEQ33838956-9D3FAB75-0216-4215-A43E-02CE60CCF0A9Q34539796-91E00E9F-F42D-4274-875D-0D8A1F6C1CB4Q36326838-370A100C-29ED-4418-B097-C383091A43D9Q36982306-5694053A-B551-48F4-BDD9-E41261AF26B6Q37594531-7BFA397B-8B2E-4D15-97CA-4FBCC3332053Q37633372-EA2DBF8E-A9B8-45E9-8B9C-08ED1ECED2B2Q38583462-9FDD666F-9773-404F-8044-57D13D044B2CQ38598073-86DD3185-396E-493A-B134-45F06390356AQ38669948-7789917D-6FC0-4EB9-8660-EE3D10CB322CQ38716317-837EC2BD-58F2-4009-A2F4-FADAA2DD40B1Q38788714-398A82B6-A1BB-4DCA-A67C-8E771DA78363Q38822073-026C85A3-1A33-4DF0-BCC1-BF9669BAF22FQ38846192-97D71C9A-C115-4262-83F8-954A444BB4D5Q38877817-69830B5C-35EB-4525-8008-F75840FCD79CQ38993825-A39E87A5-466A-45ED-B804-912E9C1C8DC7Q39014648-9B915CA1-A513-49F4-B107-222F4C4C9ACAQ39032775-FA310005-3A9E-4EA4-A360-B540022759CBQ39230418-958869B7-7057-46BC-9D73-6D2FD3FFFDB8Q42391311-5DD30AC8-7E00-4A82-B29C-EE2B3236FF5EQ45869566-96826DF7-3AD2-4D17-96C4-6866D8B80B11Q45874356-5C7B41E1-408E-4B7D-B2E8-DE80555BE641Q46208205-8F2AD2C3-9E8F-44EB-AF3F-C2A7617FC616Q46262974-200E21F8-B194-40C5-9628-8B6F7A34B98BQ47327388-96F63228-6CEC-4DD2-B009-5BF1FD9F48F7Q50897287-A7D599FE-581B-415C-9510-07735651C312Q55362738-90B78787-343D-4816-9F80-CE04D3F533C3Q57159704-DF3BB6CB-502B-48C5-8E56-2BA693345DE2Q57175584-E237E9F8-9E83-4A3A-A887-728E6928D8D3Q57952326-6E2AB22D-33C9-4755-AD22-0CE4931A6913
P2860
description
2015 nî lūn-bûn
@nan
2015 թուականի Փետրուարին հրատարակուած գիտական յօդուած
@hyw
2015 թվականի փետրվարին հրատարակված գիտական հոդված
@hy
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
name
Fanconi anemia gene editing by the CRISPR/Cas9 system.
@ast
Fanconi anemia gene editing by the CRISPR/Cas9 system.
@en
type
label
Fanconi anemia gene editing by the CRISPR/Cas9 system.
@ast
Fanconi anemia gene editing by the CRISPR/Cas9 system.
@en
prefLabel
Fanconi anemia gene editing by the CRISPR/Cas9 system.
@ast
Fanconi anemia gene editing by the CRISPR/Cas9 system.
@en
P2093
P2860
P50
P356
P1433
P1476
Fanconi anemia gene editing by the CRISPR/Cas9 system.
@en
P2093
Anthony P DeFeo
Beau R Webber
Bruce R Blazar
Christof von Kalle
J Keith Joung
John E Wagner
Jordan Jarjour
Manfred Schmidt
Mark J Osborn
Richard Gabriel
P2860
P304
P356
10.1089/HUM.2014.111
P577
2015-02-01T00:00:00Z