Normalization and improvement of CNS deficits in mice with Hurler syndrome after long-term peripheral delivery of BBB-targeted iduronidase.
about
Transcranial pulsed ultrasound facilitates brain uptake of laronidase in enzyme replacement therapy for Mucopolysaccharidosis type I diseaseToward reducing immunogenicity of enzyme replacement therapy: altering the specificity of human β-glucuronidase to compensate for α-iduronidase deficiency.Progression of Behavioral and CNS Deficits in a Viable Murine Model of Chronic Neuronopathic Gaucher Disease.Hematopoietic Stem cell transplantation and lentiviral vector-based gene therapy for Krabbe's disease: Present convictions and future prospects.Brain-targeted stem cell gene therapy corrects mucopolysaccharidosis type II via multiple mechanisms.Getting the Most: Enhancing Efficacy by Promoting Erythropoiesis and Thrombopoiesis after Gene Therapy in Mice with Hurler Syndrome
P2860
Normalization and improvement of CNS deficits in mice with Hurler syndrome after long-term peripheral delivery of BBB-targeted iduronidase.
description
2014 nî lūn-bûn
@nan
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
2014年论文
@zh
2014年论文
@zh-cn
name
Normalization and improvement ...... y of BBB-targeted iduronidase.
@ast
Normalization and improvement ...... y of BBB-targeted iduronidase.
@en
type
label
Normalization and improvement ...... y of BBB-targeted iduronidase.
@ast
Normalization and improvement ...... y of BBB-targeted iduronidase.
@en
prefLabel
Normalization and improvement ...... y of BBB-targeted iduronidase.
@ast
Normalization and improvement ...... y of BBB-targeted iduronidase.
@en
P2093
P2860
P356
P1433
P1476
Normalization and improvement ...... y of BBB-targeted iduronidase.
@en
P2093
Jing-Fen Han
Roscoe O Brady
Salim S El-Amouri
P2860
P304
P356
10.1038/MT.2014.152
P577
2014-08-04T00:00:00Z