Long-term expression of human coagulation factor VIII and correction of hemophilia A after in vivo retroviral gene transfer in factor VIII-deficient mice.
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Gene therapy for haemophiliaGene therapy for haemophiliaHemophilia A: an ideal disease to correct in uteroAnimal models of hemophiliaGene therapy for hemophiliaTherapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs.Concordant activity of transgene expression cassettes inserted into E1, E3 and E4 cloning sites in the adenovirus genome.Comparison of factor VIII transgenes bioengineered for improved expression in gene therapy of hemophilia AGene therapy for the hemophilias.Absence of a desmopressin response after therapeutic expression of factor VIII in hemophilia A dogs with liver-directed neonatal gene therapy.Gene therapy of hepatic diseases: prospects for the new millennium.RH10 provides superior transgene expression in mice when compared with natural AAV serotypes for neonatal gene therapy.Gene therapy: a 2001 perspective.Haemophilias: advances towards genetic engineering replacement therapy.Gene therapy for haemophilia: the end of a 'royal pathology' in the third millennium?Gene therapy for haemophilia.The concept of idiotypic vaccination against factor VIII inhibitors in haemophilia A.Parvovirus-mediated gene transfer for the haemophilias.Pathophysiology of inhibitors to factor VIII in patients with haemophilia A.In vivo expansion of regulatory T cells with IL-2/IL-2 mAb complexes prevents anti-factor VIII immune responses in hemophilia A mice treated with factor VIII plasmid-mediated gene therapy.piggyBac-mediated phenotypic correction of factor VIII deficiencyPerinatal gene transfer to the liver.Evaluation of transduction properties of an adenovirus vector in neonatal mice.Regional intravascular delivery of AAV-2-F.IX to skeletal muscle achieves long-term correction of hemophilia B in a large animal modelPersistent expression of factor VIII in vivo following nonprimate lentiviral gene transfer.Immunomodulation of transgene responses following naked DNA transfer of human factor VIII into hemophilia A micePreclinical and clinical gene therapy for haemophilia.AAV-based neonatal gene therapy for hemophilia A: long-term correction and avoidance of immune responses in miceGene transfer for hemophilia: can therapeutic efficacy in large animals be safely translated to patients?Tolerance induction by viral in vivo gene transferGene therapy for treatment of inherited haematological disorders.Cellular and genetic therapies for haemophilia.Genetic engineering for haemophilia A.Pharmacokinetics and pharmacodynamics of SCT800, a new recombinant FVIII, in hemophilia A mice.Gene therapy, bioengineered clotting factors and novel technologies for hemophilia treatment.Transient blockade of the inducible costimulator pathway generates long-term tolerance to factor VIII after nonviral gene transfer into hemophilia A miceGene therapy for inborn errors of liver metabolism: progress towards clinical applicationsAnti-CD3 antibodies modulate anti-factor VIII immune responses in hemophilia A mice after factor VIII plasmid-mediated gene therapy.Unique strategies for therapeutic gene transfer in haemophilia A and haemophilia BWFH State-of-the-Art Session on Therapeutic Gene Transfer Buenos Aires, Argentina.Immunomodulation for inhibitors in hemophilia A: the important role of Treg cells
P2860
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P2860
Long-term expression of human coagulation factor VIII and correction of hemophilia A after in vivo retroviral gene transfer in factor VIII-deficient mice.
description
1999 nî lūn-bûn
@nan
1999年の論文
@ja
1999年論文
@yue
1999年論文
@zh-hant
1999年論文
@zh-hk
1999年論文
@zh-mo
1999年論文
@zh-tw
1999年论文
@wuu
1999年论文
@zh
1999年论文
@zh-cn
name
Long-term expression of human ...... in factor VIII-deficient mice.
@ast
Long-term expression of human ...... in factor VIII-deficient mice.
@en
type
label
Long-term expression of human ...... in factor VIII-deficient mice.
@ast
Long-term expression of human ...... in factor VIII-deficient mice.
@en
prefLabel
Long-term expression of human ...... in factor VIII-deficient mice.
@ast
Long-term expression of human ...... in factor VIII-deficient mice.
@en
P2093
P2860
P921
P356
P1476
Long-term expression of human ...... in factor VIII-deficient mice.
@en
P2093
I Goovaerts
M L Vanderhaeghen
T VandenDriessche
V Vanslembrouck
P2860
P304
10379-10384
P356
10.1073/PNAS.96.18.10379
P407
P577
1999-08-01T00:00:00Z