Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
about
Role of the vector genome and underlying factor IX mutation in immune responses to AAV gene therapy for hemophilia BGene therapy for haemophiliaGene therapy for haemophiliaTargeted DNA mutagenesis for the cure of chronic viral infectionsAAV-mediated liver-specific MPV17 expression restores mtDNA levels and prevents diet-induced liver failureClinical development of gene therapy: results and lessons from recent successesIn utero stem cell transplantation and gene therapy: rationale, history, and recent advances toward clinical applicationThe therapeutic potential of genome editing for β-thalassemiaTargeted approaches to induce immune tolerance for Pompe disease therapyMegakaryocyte- and megakaryocyte precursor-related gene therapiesGene therapy: progress and predictionsEmerging and future therapies for hemophiliaAdeno-associated Virus as a Mammalian DNA VectorGene therapy for cardiovascular disease: advances in vector development, targeting, and delivery for clinical translationMitochondrial diseases caused by toxic compound accumulation: from etiopathology to therapeutic approachesDecoding mechanisms by which silent codon changes influence protein biogenesis and functionDevelopments in the treatment of hemophilia B: focus on emerging gene therapyThe gene therapy journey for hemophilia: are we there yet?Prospects for gene transfer for clinical heart failureParkinson's disease gene therapy: success by design meets failure by efficacyHemophilia A: an ideal disease to correct in uteroPerinatal systemic gene delivery using adeno-associated viral vectorsParvovirus glycan interactionsmiR-122 is a unique molecule with great potential in diagnosis, prognosis of liver disease, and therapy both as miRNA mimic and antimirGene doping: gene delivery for olympic victoryHuman pluripotent stem cells for modelling human liver diseases and cell therapyGene therapy on the moveGene therapy of inherited retinal degenerations: prospects and challengesCurrent translational and clinical practices in hematopoietic cell and gene therapyPresent and future challanges in the treatment of haemophilia: a clinician's perspectiveAdeno-associated virus-mediated cancer gene therapy: current statusSystemic AAV9 gene transfer in adult GM1 gangliosidosis mice reduces lysosomal storage in CNS and extends lifespan.AAV-Delivered Antibody Mediates Significant Protective Effects against SIVmac239 Challenge in the Absence of Neutralizing ActivityPredictors of hepatitis B cure using gene therapy to deliver DNA cleavage enzymes: a mathematical modeling approachPorcine model of hemophilia AElectron microscopy analysis of a disaccharide analog complex reveals receptor interactions of adeno-associated virusStructure of AAV-DJ, a Retargeted Gene Therapy Vector: Cryo-Electron Microscopy at 4.5 Å ResolutionThe structure of AAVrh32.33, a novel gene delivery vectorCurrent animal models of hemophilia: the state of the artOnce-weekly prophylactic dosing of recombinant factor IX improves adherence in hemophilia B
P2860
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P2860
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
description
2011 nî lūn-bûn
@nan
2011年の論文
@ja
2011年論文
@yue
2011年論文
@zh-hant
2011年論文
@zh-hk
2011年論文
@zh-mo
2011年論文
@zh-tw
2011年论文
@wuu
2011年论文
@zh
2011年论文
@zh-cn
name
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
@ast
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
@en
type
label
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
@ast
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
@en
prefLabel
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
@ast
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
@en
P2093
P2860
P50
P921
P356
P1476
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
@en
P2093
Amit C Nathwani
Andrew M Davidoff
Anne Riddell
Arnulfo Jaquilmac Pie
Arthur W Nienhuis
Bertil Glader
Catherine Y C Ng
Cecilia Rosales
Chris Harrington
Christopher L Morton
P2860
P304
P356
10.1056/NEJMOA1108046
P407
P577
2011-12-10T00:00:00Z