about
Targeted gene transfer to the brain via the delivery of brain-penetrating DNA nanoparticles with focused ultrasound.Integrase-Deficient Lentiviral Vector as an All-in-One Platform for Highly Efficient CRISPR/Cas9-Mediated Gene EditingGene suppression strategies for dominantly inherited neurodegenerative diseases: lessons from Huntington's disease and spinocerebellar ataxia.Sponge-mediated lentivirus delivery to acute and chronic spinal cord injuries.Microglia-specific targeting by novel capsid-modified AAV6 vectors.Hypothalamic leptin gene therapy reduces body weight without accelerating age-related bone loss.Targeting the gastrointestinal tract with viral vectors: state of the art and possible applications in research and therapy.Epigenome Editing in the Brain.AAV-mediated expression of anti-tau scFvs decreases tau accumulation in a mouse model of tauopathy.Characterization of a novel adeno-associated viral vector with preferential oligodendrocyte tropism.Timing of Gene Therapy Interventions: The Earlier, the Better.Gene suppression approaches to neurodegeneration.Ablating N-acetylaspartate prevents leukodystrophy in a Canavan disease model.Recent progress and considerations for AAV gene therapies targeting the central nervous system.Translation of MicroRNA-Based Huntingtin-Lowering Therapies from Preclinical Studies to the Clinic.New Tools for Epilepsy Therapy.Gene therapy for Rett syndrome: prospects and challenges
P2860
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P2860
description
2014 nî lūn-bûn
@nan
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
2014年论文
@zh
2014年论文
@zh-cn
name
Clinical applications involving CNS gene transfer.
@ast
Clinical applications involving CNS gene transfer.
@en
type
label
Clinical applications involving CNS gene transfer.
@ast
Clinical applications involving CNS gene transfer.
@en
prefLabel
Clinical applications involving CNS gene transfer.
@ast
Clinical applications involving CNS gene transfer.
@en
P2093
P2860
P1433
P1476
Clinical applications involving CNS gene transfer.
@en
P2093
Boris Kantor
Paola Leone
Steven J Gray
Thomas McCown
P2860
P304
P356
10.1016/B978-0-12-800149-3.00002-0
P577
2014-01-01T00:00:00Z