CRISPR/dCas9-mediated Transcriptional Inhibition Ameliorates the Epigenetic Dysregulation at D4Z4 and Represses DUX4-fl in FSH Muscular Dystrophy.
about
Multiplex gene regulation by CRISPR-ddCpf1Large family cohorts of lymphoblastoid cells provide a new cellular model for investigating facioscapulohumeral muscular dystrophy.A cross sectional study of two independent cohorts identifies serum biomarkers for facioscapulohumeral muscular dystrophy (FSHD).Nuclear bodies reorganize during myogenesis in vitro and are differentially disrupted by expression of FSHD-associated DUX4.Scalpel or Straitjacket: CRISPR/Cas9 Approaches for Muscular Dystrophies.Genome engineering: a new approach to gene therapy for neuromuscular disorders.Pre-clinical Safety and Off-Target Studies to Support Translation of AAV-Mediated RNAi Therapy for FSHD.Magnetic resonance imaging in facioscapulohumeral muscular dystrophy.A cre-inducible DUX4 transgenic mouse model for investigating facioscapulohumeral muscular dystrophy.Facioscapulohumeral Muscular Dystrophy.Functional domains of the FSHD-associated DUX4 protein.Quantitative muscle MRI and ultrasound for facioscapulohumeral muscular dystrophy: complementary imaging biomarkers
P2860
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P2860
CRISPR/dCas9-mediated Transcriptional Inhibition Ameliorates the Epigenetic Dysregulation at D4Z4 and Represses DUX4-fl in FSH Muscular Dystrophy.
description
2015 nî lūn-bûn
@nan
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
2015年论文
@zh
2015年论文
@zh-cn
name
CRISPR/dCas9-mediated Transcri ...... -fl in FSH Muscular Dystrophy.
@ast
CRISPR/dCas9-mediated Transcri ...... -fl in FSH Muscular Dystrophy.
@en
type
label
CRISPR/dCas9-mediated Transcri ...... -fl in FSH Muscular Dystrophy.
@ast
CRISPR/dCas9-mediated Transcri ...... -fl in FSH Muscular Dystrophy.
@en
prefLabel
CRISPR/dCas9-mediated Transcri ...... -fl in FSH Muscular Dystrophy.
@ast
CRISPR/dCas9-mediated Transcri ...... -fl in FSH Muscular Dystrophy.
@en
P2860
P50
P356
P1433
P1476
CRISPR/dCas9-mediated Transcri ...... -fl in FSH Muscular Dystrophy.
@en
P2860
P304
P356
10.1038/MT.2015.200
P577
2015-11-03T00:00:00Z