Review of miglustat for clinical management in Gaucher disease type 1.
about
Effect of oral eliglustat on splenomegaly in patients with Gaucher disease type 1: the ENGAGE randomized clinical trial.Imaging of Gaucher disease.ELIGLUSTAT TARTRATE: Glucosylceramide Synthase Inhibitor Treatment of Type 1 Gaucher Disease.Remodeling the proteostasis network to rescue glucocerebrosidase variants by inhibiting ER-associated degradation and enhancing ER folding.Induced Pluripotent Stem Cells for Disease Modeling and Evaluation of Therapeutics for Niemann-Pick Disease Type AInduced pluripotent stem cell technology for disease modeling and drug screening with emphasis on lysosomal storage diseasesA new framework for evaluating the health impacts of treatment for Gaucher disease type 1.Therapy for lysosomal storage disorders.Cystic fibrosis transmembrane conductance regulator modulators for personalized drug treatment of cystic fibrosis: progress to date.A peptide-linked recombinant glucocerebrosidase for targeted neuronal delivery: Design, production, and assessment.Progress and potential of non-inhibitory small molecule chaperones for the treatment of Gaucher disease and its implications for Parkinson disease.Radiological aspects of Gaucher disease.Pathology and current treatment of neurodegenerative sphingolipidoses.Neural stem cells for disease modeling and evaluation of therapeutics for infantile (CLN1/PPT1) and late infantile (CLN2/TPP1) neuronal ceroid lipofuscinoses.
P2860
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P2860
Review of miglustat for clinical management in Gaucher disease type 1.
description
2008 nî lūn-bûn
@nan
2008年の論文
@ja
2008年論文
@yue
2008年論文
@zh-hant
2008年論文
@zh-hk
2008年論文
@zh-mo
2008年論文
@zh-tw
2008年论文
@wuu
2008年论文
@zh
2008年论文
@zh-cn
name
Review of miglustat for clinical management in Gaucher disease type 1.
@en
type
label
Review of miglustat for clinical management in Gaucher disease type 1.
@en
prefLabel
Review of miglustat for clinical management in Gaucher disease type 1.
@en
P2860
P356
P1476
Review of miglustat for clinical management in Gaucher disease type 1.
@en
P2093
Can Ficicioglu
P2860
P304
P356
10.2147/TCRM.S6865
P577
2008-04-01T00:00:00Z