Functional correction of neurological and somatic disorders at later stages of disease in MPS IIIA mice by systemic scAAV9-hSGSH gene delivery
about
Serum global metabolomics profiling reveals profound metabolic impairments in patients with MPS IIIA and MPS IIIB.Gene therapy for a mouse model of glucose transporter-1 deficiency syndrome.Timing of Gene Therapy Interventions: The Earlier, the Better.Gene therapy for Mucopolysaccharidoses.Overcoming Limitations Inherent in Sulfamidase to Improve Mucopolysaccharidosis IIIA Gene Therapy.Urinary bladder extracellular matrix hydrogels and matrix-bound vesicles differentially regulate central nervous system neuron viability and axon growth and branching.Recent progress and considerations for AAV gene therapies targeting the central nervous system.Targeting Root Cause by Systemic scAAV9-h Gene Delivery: Functional Correction and Reversal of Severe MPS II in Mice
P2860
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P2860
Functional correction of neurological and somatic disorders at later stages of disease in MPS IIIA mice by systemic scAAV9-hSGSH gene delivery
description
2016 nî lūn-bûn
@nan
2016年の論文
@ja
2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
2016年论文
@zh
2016年论文
@zh-cn
name
Functional correction of neuro ...... mic scAAV9-hSGSH gene delivery
@en
type
label
Functional correction of neuro ...... mic scAAV9-hSGSH gene delivery
@en
prefLabel
Functional correction of neuro ...... mic scAAV9-hSGSH gene delivery
@en
P2093
P2860
P356
P1476
Functional correction of neuro ...... mic scAAV9-hSGSH gene delivery
@en
P2093
Aaron S Meadows
Darren A Murrey
Douglas M McCarty
Kimberly Zaraspe
Marcela P Cataldi
Tierra A Ware
P2860
P356
10.1038/MTM.2016.36
P577
2016-06-08T00:00:00Z