Multi-exon Skipping Using Cocktail Antisense Oligonucleotides in the Canine X-linked Muscular Dystrophy.
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The golden retriever model of Duchenne muscular dystrophy.LNA/DNA mixmer-based antisense oligonucleotides correct alternative splicing of the SMN2 gene and restore SMN protein expression in type 1 SMA fibroblastsDesigning Effective Antisense Oligonucleotides for Exon Skipping.The potential of antisense oligonucleotide therapies for inherited childhood lung diseases.Skipping Multiple Exons to Treat DMD-Promises and Challenges.
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Multi-exon Skipping Using Cocktail Antisense Oligonucleotides in the Canine X-linked Muscular Dystrophy.
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article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 24 May 2016
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Multi-exon Skipping Using Cock ...... e X-linked Muscular Dystrophy.
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Multi-exon Skipping Using Cock ...... e X-linked Muscular Dystrophy.
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type
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Multi-exon Skipping Using Cock ...... e X-linked Muscular Dystrophy.
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Multi-exon Skipping Using Cock ...... e X-linked Muscular Dystrophy.
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prefLabel
Multi-exon Skipping Using Cock ...... e X-linked Muscular Dystrophy.
@en
Multi-exon Skipping Using Cock ...... e X-linked Muscular Dystrophy.
@nl
P2093
P2860
P356
P1476
Multi-exon Skipping Using Cock ...... e X-linked Muscular Dystrophy.
@en
P2093
Bailey Miskew Nichols
Joshua J A Lee
Mutsuki Kuraoka
Shin'ichi Takeda
Toshifumi Yokota
Yoshitsugu Aoki
P2860
P356
10.3791/53776
P577
2016-05-24T00:00:00Z