Development of gene therapy for blood disorders: an update.
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Customizing the genome as therapy for the β-hemoglobinopathiesTargeted Gene Correction in Osteopetrotic-Induced Pluripotent Stem Cells for the Generation of Functional OsteoclastsState-of-the-art human gene therapy: part II. Gene therapy strategies and clinical applications.Therapeutic applications of extracellular vesicles: clinical promise and open questions.Hepatocyte Heparan Sulfate Is Required for Adeno-Associated Virus 2 but Dispensable for Adenovirus 5 Liver Transduction In Vivo.Functional Restoration of gp91phox-Oxidase Activity by BAC Transgenesis and Gene Targeting in X-linked Chronic Granulomatous Disease iPSCs.Agammaglobulinemia: causative mutations and their implications for novel therapies.Avoiding immunological rejection in regenerative medicine.New approaches to gene and cell therapy for hemophilia.Non-integrating gamma-retroviral vectors as a versatile tool for transient zinc-finger nuclease delivery.CRISPR-Cas9 technology and its application in haematological disorders.Cure for thalassemia major - from allogeneic hematopoietic stem cell transplantation to gene therapy.Pseudotyped murine leukemia virus for schistosome transgenesis: approaches, methods and perspectives.Lentiviral Transfer of γ-Globin with Fusion Gene NUP98-HOXA10HD Expands Hematopoietic Stem Cells and Ameliorates Murine β-Thalassemia.High-level production of replication-defective human immunodeficiency type 1 virus vector particles using helper-dependent adenovirus vectors.Short-course rapamycin treatment enables engraftment of immunogenic gene-engineered bone marrow under low-dose irradiation to permit long-term immunological tolerance.Developments in Hematopoietic Stem Cell Expansion and Gene Editing Technologies.Transfection by cationic gemini lipids and surfactants
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Development of gene therapy for blood disorders: an update.
description
article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 10 July 2013
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Development of gene therapy for blood disorders: an update.
@en
Development of gene therapy for blood disorders: an update.
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type
label
Development of gene therapy for blood disorders: an update.
@en
Development of gene therapy for blood disorders: an update.
@nl
prefLabel
Development of gene therapy for blood disorders: an update.
@en
Development of gene therapy for blood disorders: an update.
@nl
P2860
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Development of gene therapy for blood disorders: an update.
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Arthur W Nienhuis
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P304
P356
10.1182/BLOOD-2013-04-453209
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P577
2013-07-10T00:00:00Z