Efficacy and biodistribution analysis of intracerebroventricular administration of an optimized scAAV9-SMN1 vector in a mouse model of spinal muscular atrophy.
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Efficacy and biodistribution analysis of intracerebroventricular administration of an optimized scAAV9-SMN1 vector in a mouse model of spinal muscular atrophy.
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article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 14 September 2016
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Efficacy and biodistribution a ...... el of spinal muscular atrophy.
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Efficacy and biodistribution a ...... el of spinal muscular atrophy.
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type
label
Efficacy and biodistribution a ...... el of spinal muscular atrophy.
@en
Efficacy and biodistribution a ...... el of spinal muscular atrophy.
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prefLabel
Efficacy and biodistribution a ...... el of spinal muscular atrophy.
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Efficacy and biodistribution a ...... el of spinal muscular atrophy.
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P2093
P2860
P356
P1476
Efficacy and biodistribution a ...... del of spinal muscular atrophy
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P2093
Alban Vignaud
Ana Buj-Bello
Annalisa Lattanzi
Bernard Gjata
Laetitia Van Wittenberghe
Martine Barkats
Matthieu Jeavons
Nicole Armbruster
Samia Martin
Thibaut Marais
P2860
P356
10.1038/MTM.2016.60
P577
2016-09-14T00:00:00Z