Current Challenges and Future Directions in Recombinant AAV-Mediated Gene Therapy of Duchenne Muscular Dystrophy. - Wikidata - awgldk - TriplyDB

Current Challenges and Future Directions in Recombinant AAV-Mediated Gene Therapy of Duchenne Muscular Dystrophy.

Current Challenges and Future Directions in Recombinant AAV-Mediated Gene Therapy of Duchenne Muscular Dystrophy.

http://www.wikidata.org/entity/Q37277411

about

Current and emerging treatment strategies for Duchenne muscular dystrophy Pharmacology of manipulating lean body mass X-Linked Dilated Cardiomyopathy: A Cardiospecific Phenotype of Dystrophinopathy.Treatment of hypophosphatasia by muscle-directed expression of bone-targeted alkaline phosphatase via self-complementary AAV8 vector.Current Translational Research and Murine Models For Duchenne Muscular Dystrophy.CRISPR/Cas9-mediated correction of human genetic disease.Moving towards successful exon-skipping therapy for Duchenne muscular dystrophy.Precise correction of the dystrophin gene in duchenne muscular dystrophy patient induced pluripotent stem cells by TALEN and CRISPR-Cas9.An Overview of Recent Therapeutics Advances for Duchenne Muscular Dystrophy.Chemotherapeutics overcoming nonsense mutation-associated genetic diseases: medicinal chemistry of negamycin.Myopenia and precision (P4) medicine.Structure-Activity Relationship Study of Leucyl-3-epi-deoxynegamycin for Potent Premature Termination Codon Readthrough.Bone-Targeted Alkaline Phosphatase Treatment of Mandibular Bone and Teeth in Lethal Hypophosphatasia via an scAAV8 Vector

P2860

Q26741535-B1E98FEC-AF45-4D6C-9E60-7DF55EE69034 Q26824503-3ED2D36D-A42C-4CB7-B2C4-3906C167AFCD Q35818371-A20209B9-0D42-467B-98F7-8F431B49EBE0 Q36538166-ABE1176C-1AD7-456A-88DE-017F92E2CB03 Q37610505-2C502B16-3D25-4FD9-811E-A386054E1A02 Q39324185-C5500735-56F1-4999-B08B-AD0B4327F529 Q39342422-2D9FA709-2AB1-443C-A528-0827E496CFC6 Q41873090-536BBBDB-19A8-4394-BEDB-A11EE8839DB6 Q47607031-F0668047-1696-422A-BF45-CE3F5DF279EE Q47738762-A759506D-3A92-4D11-B074-8F0FECDD256B Q49859737-BB485095-499F-4A7F-9D6A-AAAF0F81D475 Q50066093-830B929B-FAE1-4D17-8F96-8F098BF64FEB Q57168626-A8439B26-4C6B-44E3-9C1C-F5142CC3315B

P2860

Current Challenges and Future Directions in Recombinant AAV-Mediated Gene Therapy of Duchenne Muscular Dystrophy.

http://www.wikidata.org/entity/Q37277411

description

article científic

@ca

article scientifique

@fr

articolo scientifico

@it

artigo científico

@pt

bilimsel makale

@tr

scientific article published on 27 June 2013

@en

vedecký článok

@sk

vetenskaplig artikel

@sv

videnskabelig artikel

@da

vědecký článek

@cs

name

Current Challenges and Future ...... f Duchenne Muscular Dystrophy.

@en

Current Challenges and Future ...... f Duchenne Muscular Dystrophy.

@nl

type

label

Current Challenges and Future ...... f Duchenne Muscular Dystrophy.

@en

Current Challenges and Future ...... f Duchenne Muscular Dystrophy.

@nl

prefLabel

Current Challenges and Future ...... f Duchenne Muscular Dystrophy.

@en

Current Challenges and Future ...... f Duchenne Muscular Dystrophy.

@nl

P1433

Q37277411-FF2FAE68-6650-4610-918C-44D024D360C1

P1476

Q37277411-BB266B7A-0F06-4680-8BA0-B63C608E54C2

P2093

Q37277411-30FB85A1-8E0B-4450-A00C-E7B6F73E8A96

Q37277411-353F90D1-62F6-4496-86AE-C669AC7CE337

P2860

Q37277411-02F0A212-8EF3-4BC9-AFE8-482715D7256D

Q37277411-03A03B78-3FEF-44FF-AA52-19CD8D833F63

Q37277411-05924B3E-1CF3-49A9-9EEC-CD1760B4038E

Q37277411-08474D55-2566-4551-8E6E-DA17B7590225

Q37277411-0A7FAC36-AE33-494F-ACE7-9893922812AD

Q37277411-0BFE3C57-4668-4CA7-901F-3669F7E141CD

Q37277411-0C80DF8B-18B9-48EC-9F40-4E7ABA05E08E

Q37277411-0E1CCCCA-323C-4ACC-BB06-0D8498E173E9

Q37277411-0EA454FC-1B20-4BBA-BB48-F0C0529BA3BF

Q37277411-108F1C69-2790-49B8-A3A6-5A8CFD849941

P304

Q37277411-8118FC94-3D8B-47C1-B12C-21E0FBE74E82

P31

Q37277411-A70045D5-4695-49A6-90E4-0B470165EAF3

P356

Q37277411-D417BC5E-8DD9-4986-A8D2-862D88C05B1A

P433

Q37277411-03DDC343-3C31-4476-B991-562BE8934172

P478

Q37277411-2701A8F6-915A-4BA5-A239-4C0DE55674A8

P577

Q37277411-E3456AB4-61E3-4A04-A64A-BCD52E324BF3

P5875

Q37277411-2C903BCF-E9EA-4CB0-9515-3C896E1B3755

P698

Q37277411-C3F381C2-C193-4431-90CE-4DC59F19FDDD

P921

Q37277411-C7B85FD2-B9F5-4CDF-ADD1-13ACE2B950E3

P932

Q37277411-2E79BD53-DEC1-44CB-9C61-991033104149

P356

P1433

Pharmaceuticals

P1476

Current Challenges and Future ...... f Duchenne Muscular Dystrophy.

@en

P2093

Shin'ichi Takeda

http://www.w3.org/2001/XMLSchema#string

Takashi Okada

http://www.w3.org/2001/XMLSchema#string

P2860

Biochemical evidence for association of dystrobrevin with the sarcoglycan-sarcospan complex as a basis for understanding sarcoglycanopathy

Drug treatment of Duchenne muscular dystrophy: available evidence and perspectives

A highly stable and nonintegrated human artificial chromosome (HAC) containing the 2.4 Mb entire human dystrophin gene

Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study

Population frequencies of inherited neuromuscular diseases--a world survey

Mesoangioblast stem cells ameliorate muscle function in dystrophic dogs

Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping

Daily treatment with SMTC1100, a novel small molecule utrophin upregulator, dramatically reduces the dystrophic symptoms in the mdx mouse

Dystrophin: the protein product of the Duchenne muscular dystrophy locus

P304

813-836

http://www.w3.org/2001/XMLSchema#string

P31

scholarly article

P356

10.3390/PH6070813

http://www.w3.org/2001/XMLSchema#string

P433

7

http://www.w3.org/2001/XMLSchema#string

P478

6

http://www.w3.org/2001/XMLSchema#string

P577

2013-06-27T00:00:00Z

http://www.w3.org/2001/XMLSchema#dateTime

P5875

258922764

http://www.w3.org/2001/XMLSchema#string

P698

24276316

http://www.w3.org/2001/XMLSchema#string

P921

P932

3816704

http://www.w3.org/2001/XMLSchema#string