Impact of long-term elosulfase alfa treatment on respiratory function in patients with Morquio A syndrome.
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Elosulfase alfa (BMN 110) for the treatment of mucopolysaccharidosis IVA (Morquio A Syndrome).Minimal clinically important difference for the 6-min walk test: literature review and application to Morquio A syndrome.Impact of elosulfase alfa in patients with morquio A syndrome who have limited ambulation: An open-label, phase 2 study.
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Impact of long-term elosulfase alfa treatment on respiratory function in patients with Morquio A syndrome.
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article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 23 August 2016
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Impact of long-term elosulfase ...... ients with Morquio A syndrome.
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Impact of long-term elosulfase ...... ients with Morquio A syndrome.
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type
label
Impact of long-term elosulfase ...... ients with Morquio A syndrome.
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Impact of long-term elosulfase ...... ients with Morquio A syndrome.
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Impact of long-term elosulfase ...... ients with Morquio A syndrome.
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Impact of long-term elosulfase ...... ients with Morquio A syndrome.
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P2860
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P1476
Impact of long-term elosulfase ...... tients with Morquio A syndrome
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Barbara K Burton
Celeste Decker
Elaina Jurecki
Fiona Stewart
Julian Raiman
Moeenaldeen D AlSayed
Norberto Guelbert
Paul R Harmatz
Robert Matousek
Roberto Giugliani
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P2888
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P356
10.1007/S10545-016-9973-6
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2016-08-23T00:00:00Z