Gene therapy in large animal models of muscular dystrophy.
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Man's best friend becomes biology's best in show: genome analyses in the domestic dogDog models of naturally occurring cancerPersistent expression of FLAG-tagged micro dystrophin in nonhuman primates following intramuscular and vascular delivery.Immune responses to AAV in canine muscle monitored by cellular assays and noninvasive imaging.Gene therapy in large animal models of human genetic diseases. IntroductionProtein replacement therapy and gene transfer in canine models of hemophilia A, hemophilia B, von willebrand disease, and factor VII deficiency.Safety of liver gene transfer following peripheral intravascular delivery of adeno-associated virus (AAV)-5 and AAV-6 in a large animal modelImmune Responses to rAAV6: The Influence of Canine Parvovirus Vaccination and Neonatal Administration of Viral VectorLong-term systemic myostatin inhibition via liver-targeted gene transfer in golden retriever muscular dystrophy.Long-term engraftment of multipotent mesenchymal stromal cells that differentiate to form myogenic cells in dogs with Duchenne muscular dystrophyA COLQ Missense Mutation in Sphynx and Devon Rex Cats with Congenital Myasthenic SyndromeLong-term restoration of cardiac dystrophin expression in golden retriever muscular dystrophy following rAAV6-mediated exon skippingThe correlation analysis of functional factors and age with duchenne muscular dystrophy.Impacts of dystrophin and utrophin domains on actin structural dynamics: implications for therapeutic design.Successful regional delivery and long-term expression of a dystrophin gene in canine muscular dystrophy: a preclinical model for human therapies.Use of Adeno-Associated Virus to Enrich Cardiomyocytes Derived from Human Stem Cells.Non-Targeted Metabolomics Analysis of Golden Retriever Muscular Dystrophy-Affected Muscles Reveals Alterations in Arginine and Proline Metabolism, and Elevations in Glutamic and Oleic Acid In Vivo.Myelination is delayed during postnatal brain development in the mdx mouse model of Duchenne muscular dystrophyMultiple Species Comparison of Cardiac Troponin T and Dystrophin: Unravelling the DNA behind Dilated Cardiomyopathy.At the Crossroads of Clinical and Preclinical Research for Muscular Dystrophy-Are We Closer to Effective Treatment for Patients?
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P2860
Gene therapy in large animal models of muscular dystrophy.
description
article científic
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article scientifique
@fr
articolo scientifico
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artigo científico
@pt
bilimsel makale
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scientific article published on January 2009
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vedecký článok
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vetenskaplig artikel
@sv
videnskabelig artikel
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vědecký článek
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name
Gene therapy in large animal models of muscular dystrophy.
@en
Gene therapy in large animal models of muscular dystrophy.
@nl
type
label
Gene therapy in large animal models of muscular dystrophy.
@en
Gene therapy in large animal models of muscular dystrophy.
@nl
prefLabel
Gene therapy in large animal models of muscular dystrophy.
@en
Gene therapy in large animal models of muscular dystrophy.
@nl
P2093
P2860
P356
P1433
P1476
Gene therapy in large animal models of muscular dystrophy.
@en
P2093
Jeffrey S Chamberlain
Stephen J Tapscott
Zejing Wang
P2860
P304
P356
10.1093/ILAR.50.2.187
P577
2009-01-01T00:00:00Z