Enzyme replacement therapy "drug holiday": results from an unexpected shortage of an orphan drug supply in Australia.
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Enzyme replacement and substrate reduction therapy for Gaucher diseaseCost-effectiveness of enzyme replacement therapy for type 1 Gaucher disease.Impact of imiglucerase supply shortage on clinical and laboratory parameters in Norrbottnian patients with Gaucher disease type 3Consequences of a global enzyme shortage of agalsidase beta in adult Dutch Fabry patients.Impact of imiglucerase supply constraint on the therapeutic management and course of disease in French patients with Gaucher disease type 1Did the temporary shortage in supply of imiglucerase have clinical consequences? Retrospective observational study on 34 italian Gaucher type I patients.Effects of switching from a reduced dose imiglucerase to velaglucerase in type 1 Gaucher disease: clinical and biochemical outcomesRecent advances and novel treatments for sphingolipidoses.Adeno-associated viral gene therapy for mucopolysaccharidoses exhibiting neurodegeneration.Medicine shortages in Australia: causes, impact and management strategies in the community setting.
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P2860
Enzyme replacement therapy "drug holiday": results from an unexpected shortage of an orphan drug supply in Australia.
description
article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on June 2010
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Enzyme replacement therapy "dr ...... phan drug supply in Australia.
@en
Enzyme replacement therapy "dr ...... phan drug supply in Australia.
@nl
type
label
Enzyme replacement therapy "dr ...... phan drug supply in Australia.
@en
Enzyme replacement therapy "dr ...... phan drug supply in Australia.
@nl
prefLabel
Enzyme replacement therapy "dr ...... phan drug supply in Australia.
@en
Enzyme replacement therapy "dr ...... phan drug supply in Australia.
@nl
P2093
P921
P1476
Enzyme replacement therapy "dr ...... phan drug supply in Australia.
@en
P2093
Jack Goldblatt
Janice M Fletcher
Jim McGill
Meredith Wilson
P304
P356
10.1016/J.BCMD.2010.05.002
P50
P577
2010-06-01T00:00:00Z