Metabolic correction in microglia derived from Sandhoff disease model mice.
about
Is genetic rescue of cystinosis an achievable treatment goal?Production of recombinant beta-hexosaminidase A, a potential enzyme for replacement therapy for Tay-Sachs and Sandhoff diseases, in the methylotrophic yeast Ogataea minutaHematopoietic stem cell gene therapy for the multisystemic lysosomal storage disorder cystinosis.Anti-inflammatory Therapy With Simvastatin Improves Neuroinflammation and CNS Function in a Mouse Model of Metachromatic LeukodystrophyAAV-mediated gene delivery attenuates neuroinflammation in feline Sandhoff disease.Introduction of an N-glycan sequon into HEXA enhances human beta-hexosaminidase cellular uptake in a model of Sandhoff disease.Reversion of the biochemical defects in murine embryonic Sandhoff neurons using a bicistronic lentiviral vector encoding hexosaminidase alpha and beta.
P2860
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P2860
Metabolic correction in microglia derived from Sandhoff disease model mice.
description
2005 nî lūn-bûn
@nan
2005年の論文
@ja
2005年学术文章
@wuu
2005年学术文章
@zh-cn
2005年学术文章
@zh-hans
2005年学术文章
@zh-my
2005年学术文章
@zh-sg
2005年學術文章
@yue
2005年學術文章
@zh
2005年學術文章
@zh-hant
name
Metabolic correction in microglia derived from Sandhoff disease model mice.
@en
type
label
Metabolic correction in microglia derived from Sandhoff disease model mice.
@en
prefLabel
Metabolic correction in microglia derived from Sandhoff disease model mice.
@en
P2093
P2860
P1476
Metabolic correction in microglia derived from Sandhoff disease model mice.
@en
P2093
Aya Kuroki
Daisuke Tsuji
Kohji Itoh
Tomohiro Itakura
Yasuhiro Ishibashi
P2860
P304
P356
10.1111/J.1471-4159.2005.03317.X
P407
P577
2005-08-10T00:00:00Z