How We Manage Adenosine Deaminase-Deficient Severe Combined Immune Deficiency (ADA SCID).
about
Evolving Gene Therapy in Primary Immunodeficiency.Long-Term Outcome of Adenosine Deaminase-Deficient Patients-a Single-Center Experience.Adenosine Deaminase (ADA)-Deficient Severe Combined Immune Deficiency (SCID): Molecular Pathogenesis and Clinical Manifestations.Gene therapy in rare diseases: the benefits and challenges of developing a patient-centric registry for Strimvelis in ADA-SCID.Adenosine deaminase deficiency: a review.
P2860
How We Manage Adenosine Deaminase-Deficient Severe Combined Immune Deficiency (ADA SCID).
description
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name
How We Manage Adenosine Deaminase-Deficient Severe Combined Immune Deficiency (ADA SCID).
@en
How We Manage Adenosine Deaminase-Deficient Severe Combined Immune Deficiency
@nl
type
label
How We Manage Adenosine Deaminase-Deficient Severe Combined Immune Deficiency (ADA SCID).
@en
How We Manage Adenosine Deaminase-Deficient Severe Combined Immune Deficiency
@nl
prefLabel
How We Manage Adenosine Deaminase-Deficient Severe Combined Immune Deficiency (ADA SCID).
@en
How We Manage Adenosine Deaminase-Deficient Severe Combined Immune Deficiency
@nl
P2860
P1476
How We Manage Adenosine Deaminase-Deficient Severe Combined Immune Deficiency (ADA SCID).
@en
P2093
Donald B Kohn
H Bobby Gaspar
P2860
P2888
P304
P356
10.1007/S10875-017-0373-Y
P577
2017-02-14T00:00:00Z