Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

about

Getting the Most: Enhancing Efficacy by Promoting Erythropoiesis and Thrombopoiesis after Gene Therapy in Mice with Hurler Syndrome

P2860

Q58577240-F167AB98-F2E0-442B-B1D5-C7C1F7F7B5C7

P2860

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

Item

http://www.wikidata.org/entity/Q39227498

description

2017 nî lūn-bûn

@nan

2017年の論文

@ja

2017年論文

@yue

2017年論文

@zh-hant

2017年論文

@zh-hk

2017年論文

@zh-mo

2017年論文

@zh-tw

2017年论文

@wuu

2017年论文

@zh

2017年论文

@zh-cn

name

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

@en

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

@nl

type

Item

label

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

@en

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

@nl

prefLabel

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

@en

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

@nl

P1476

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

@en

P2093

Alessandra Biffi

http://www.w3.org/2001/XMLSchema#string

P2860

Genome sequence of the basal haplorrhine primate Tarsius syrichta reveals unusual insertions

In vivo protein transduction: delivery of a biologically active protein into the mouse

Correction of metachromatic leukodystrophy in the mouse model by transplantation of genetically modified hematopoietic stem cells.

Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model.

Myeloid/Microglial driven autologous hematopoietic stem cell gene therapy corrects a neuronopathic lysosomal disease

Effective intravenous therapy for neurodegenerative disease with a therapeutic enzyme and a peptide that mediates delivery to the brain

Insulin receptor antibody-sulfamidase fusion protein penetrates the primate blood-brain barrier and reduces glycosoaminoglycans in Sanfilippo type A cells.

Overcoming the blood-brain barrier with high-dose enzyme replacement therapy in murine mucopolysaccharidosis VII.

Enzyme replacement therapy and/or hematopoietic stem cell transplantation at diagnosis in patients with mucopolysaccharidosis type I: results of a European consensus procedure.

Management of neuronopathic Gaucher disease: a European consensus.

P304

1155-1162

http://www.w3.org/2001/XMLSchema#string

P31

scholarly article

P356

10.1016/J.YMTHE.2017.03.025

http://www.w3.org/2001/XMLSchema#string

P433

http://www.w3.org/2001/XMLSchema#string

P478

http://www.w3.org/2001/XMLSchema#string

P577

2017-04-04T00:00:00Z

http://www.w3.org/2001/XMLSchema#dateTime

P698

28389320

http://www.w3.org/2001/XMLSchema#string

P921

gene therapy

P932

5417839

http://www.w3.org/2001/XMLSchema#string

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

about

P2860

P2860

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

description

name

type

label

prefLabel

P1433

P1476

P2093

P2860

P304

P31

P356

P433

P478

P577

P698

P921

P932

P356

P1433

P1476

P2093

P2860

P304

P31

P356

P433

P478

P577

P698

P921

P932