Considerations for a Successful RNA Trans-splicing Repair of Genetic Disorders
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mRNA trans-splicing in gene therapy for genetic diseasesCD22ΔE12 as a molecular target for corrective repair using RNA trans-splicing: anti-leukemic activity of a rationally designed RNA trans-splicing moleculeReprogramming the Dynamin 2 mRNA by Spliceosome-mediated RNA Trans-splicing.Lessons from non-canonical splicingTrans-splicing improvement by the combined application of antisense strategies.Construction and validation of an RNA trans-splicing molecule suitable to repair a large number of COL7A1 mutations.RNA-based therapies for genodermatoses.Designing Efficient Double RNA trans-Splicing Molecules for Targeted RNA Repair.An RNA-targeted therapy for dystrophic epidermolysis bullosa.RNA Trans-Splicing Modulation via Antisense Molecule Interference.
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Considerations for a Successful RNA Trans-splicing Repair of Genetic Disorders
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2014 nî lūn-bûn
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Considerations for a Successful RNA Trans-splicing Repair of Genetic Disorders
@en
Considerations for a Successful RNA Trans-splicing Repair of Genetic Disorders.
@nl
type
label
Considerations for a Successful RNA Trans-splicing Repair of Genetic Disorders
@en
Considerations for a Successful RNA Trans-splicing Repair of Genetic Disorders.
@nl
prefLabel
Considerations for a Successful RNA Trans-splicing Repair of Genetic Disorders
@en
Considerations for a Successful RNA Trans-splicing Repair of Genetic Disorders.
@nl
P2860
P356
P1476
Considerations for a Successful RNA Trans-splicing Repair of Genetic Disorders
@en
P2093
Johann W Bauer
Verena Wally
P2860
P356
10.1038/MTNA.2014.10
P577
2014-04-08T00:00:00Z