Broad functional correction of molecular impairments by systemic delivery of scAAVrh74-hSGSH gene delivery in MPS IIIA mice.
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A Comprehensive Map of CNS Transduction by Eight Recombinant Adeno-associated Virus Serotypes Upon Cerebrospinal Fluid Administration in Pigs.Progressive neurologic and somatic disease in a novel mouse model of human mucopolysaccharidosis type IIIC.Serum global metabolomics profiling reveals profound metabolic impairments in patients with MPS IIIA and MPS IIIB.Adeno-Associated Virus-Based Gene Therapy for CNS Diseases.Phase I and II clinical trials for the mucopolysaccharidoses.
P2860
Broad functional correction of molecular impairments by systemic delivery of scAAVrh74-hSGSH gene delivery in MPS IIIA mice.
description
2015 nî lūn-bûn
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2015年の論文
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2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
2015年论文
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2015年论文
@zh-cn
name
Broad functional correction of ...... ene delivery in MPS IIIA mice.
@en
Broad functional correction of ...... ene delivery in MPS IIIA mice.
@nl
type
label
Broad functional correction of ...... ene delivery in MPS IIIA mice.
@en
Broad functional correction of ...... ene delivery in MPS IIIA mice.
@nl
prefLabel
Broad functional correction of ...... ene delivery in MPS IIIA mice.
@en
Broad functional correction of ...... ene delivery in MPS IIIA mice.
@nl
P2093
P2860
P356
P1433
P1476
Broad functional correction of ...... ene delivery in MPS IIIA mice.
@en
P2093
Aaron S Meadows
Bartholomew J Naughton
Darren A Murrey
David E Newsom
Douglas M McCarty
F Jason Duncan
Kelly Reed Clark
Kimberly Zaraspe
P2860
P304
P356
10.1038/MT.2015.9
P50
P577
2015-01-16T00:00:00Z