Clinical investigation of Duchenne muscular dystrophy. A methodology for therapeutic trials based on natural history controls.

Clinical investigation of Duchenne muscular dystrophy. A methodology for therapeutic trials based on natural history controls.

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http://www.wikidata.org/entity/Q41998658
Current understanding of molecular pathology and treatment of cardiomyopathy in duchenne muscular dystrophyClinical heterogeneity of duchenne muscular dystrophy (DMD): definition of sub-phenotypes and predictive criteria by long-term follow-up.The cooperative international neuromuscular research group Duchenne natural history study: glucocorticoid treatment preserves clinically meaningful functional milestones and reduces rate of disease progression as measured by manual muscle testing anAssessment of intramuscular lipid and metabolites of the lower leg using magnetic resonance spectroscopy in boys with Duchenne muscular dystrophy.The cooperative international neuromuscular research group Duchenne natural history study--a longitudinal investigation in the era of glucocorticoid therapy: design of protocol and the methods used.A phase 1/2a follistatin gene therapy trial for becker muscular dystrophy.Proof of concept of the ability of the kinect to quantify upper extremity function in dystrophinopathyCINRG pilot trial of coenzyme Q10 in steroid-treated Duchenne muscular dystrophy.Non-invasive evaluation of muscle disease in the canine model of Duchenne muscular dystrophy by electrical impedance myography.Motor and cognitive assessment of infants and young boys with Duchenne Muscular Dystrophy: results from the Muscular Dystrophy Association DMD Clinical Research Network.The 6-minute walk test and other endpoints in Duchenne muscular dystrophy: longitudinal natural history observations over 48 weeks from a multicenter studyMolecular genetics in muscular dystrophy research: revolutionary progress.Facioscapulohumeral muscular dystrophy: a prospective study of weakness and functional impairment.CINRG randomized controlled trial of creatine and glutamine in Duchenne muscular dystrophy.Duchenne muscular dystrophy quantification: a multivariate analysis of surface EMG.Tissue- and case-specific retention of intron 40 in mature dystrophin mRNASystemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy
P2860

Clinical investigation of Duchenne muscular dystrophy. A methodology for therapeutic trials based on natural history controls.

Item
http://www.wikidata.org/entity/Q41998658
description
1987 nî lūn-bûn
@nan
1987年の論文
@ja
1987年論文
@yue
1987年論文
@zh-hant
1987年論文
@zh-hk
1987年論文
@zh-mo
1987年論文
@zh-tw
1987年论文
@wuu
1987年论文
@zh
1987年论文
@zh-cn
name
Clinical investigation of Duch ...... d on natural history controls.
@en
type
label
Clinical investigation of Duch ...... d on natural history controls.
@en
prefLabel
Clinical investigation of Duch ...... d on natural history controls.
@en
P1433
P1476
P2093
P304
P31
P356
P433
P478
P577
P698
P356
P1433
P1476
Clinical investigation of Duch ...... d on natural history controls.
@en
P2093
P304
P31
P356
10.1001/ARCHNEUR.1987.00520200012009
P433
P478
P577
P698