Clinical and biochemical improvements in a patient with MNGIE following enzyme replacement.
about
Delivery of drugs bound to erythrocytes: new avenues for an old intravascular carrierInborn errors of pyrimidine metabolism: clinical update and therapyAllogeneic haematopoietic stem cell transplantation for mitochondrial neurogastrointestinal encephalomyopathy.Emerging therapies for mitochondrial disorders.Mitochondrial diseases: advances and issues.Approaches to erythrocyte-mediated drug delivery.Emerging aspects of treatment in mitochondrial disorders.Mitochondrial Neurogastrointestinal Encephalomyopathy Caused by Thymidine Phosphorylase Enzyme Deficiency: From Pathogenesis to Emerging Therapeutic Options.Erythrocyte-mediated delivery of recombinant enzymes.Erythrocytes as Carriers for Drug Delivery in Blood Transfusion and Beyond.Drug delivery by erythrocytes: "Primum non nocere".Long-Term Restoration of Thymidine Phosphorylase Function and Nucleoside Homeostasis Using Hematopoietic Gene Therapy in a Murine Model of Mitochondrial Neurogastrointestinal Encephalomyopathy.Diagnosis of mitochondrial neurogastrointestinal encephalomyopathy: proposal of a clinical algorithm.Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE.Validation of an Immunoassay for Anti-thymidine Phosphorylase Antibodies in Patients with MNGIE Treated with Enzyme Replacement Therapy
P2860
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P2860
Clinical and biochemical improvements in a patient with MNGIE following enzyme replacement.
description
2013 nî lūn-bûn
@nan
2013年の論文
@ja
2013年論文
@yue
2013年論文
@zh-hant
2013年論文
@zh-hk
2013年論文
@zh-mo
2013年論文
@zh-tw
2013年论文
@wuu
2013年论文
@zh
2013年论文
@zh-cn
name
Clinical and biochemical impro ...... following enzyme replacement.
@en
Clinical and biochemical impro ...... following enzyme replacement.
@nl
type
label
Clinical and biochemical impro ...... following enzyme replacement.
@en
Clinical and biochemical impro ...... following enzyme replacement.
@nl
prefLabel
Clinical and biochemical impro ...... following enzyme replacement.
@en
Clinical and biochemical impro ...... following enzyme replacement.
@nl
P2093
P2860
P1433
P1476
Clinical and biochemical impro ...... following enzyme replacement.
@en
P2093
Bridget E Bax
Mauro Scarpelli
Murray D Bain
Nicholas Moran
Paola Tonin
P2860
P304
P356
10.1212/WNL.0B013E3182A6CB4B
P407
P577
2013-08-21T00:00:00Z