Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.

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Functional correction of dystrophin actin binding domain mutations by genome editing.Correction of diverse muscular dystrophy mutations in human engineered heart muscle by single-site genome editing.An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype

P2860

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P2860

Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.

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http://www.wikidata.org/entity/Q42094546

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2017 nî lūn-bûn

@nan

2017年の論文

@ja

2017年論文

@yue

2017年論文

@zh-hant

2017年論文

@zh-hk

2017年論文

@zh-mo

2017年論文

@zh-tw

2017年论文

@wuu

2017年论文

@zh

2017年论文

@zh-cn

name

Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.

@en

Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.

@nl

type

Item

label

Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.

@en

Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.

@nl

prefLabel

Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.

@en

Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.

@nl

P1476

Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System

@en

P2093

Annalisa Lattanzi

http://www.w3.org/2001/XMLSchema#string

Araksya Izmiryan

http://www.w3.org/2001/XMLSchema#string

Arianna Moiani

http://www.w3.org/2001/XMLSchema#string

Elena Barbon

http://www.w3.org/2001/XMLSchema#string

Francesco Bernardi

http://www.w3.org/2001/XMLSchema#string

Kamel Mamchaoui

http://www.w3.org/2001/XMLSchema#string

Samia Martin

http://www.w3.org/2001/XMLSchema#string

Stephanie Duguez

http://www.w3.org/2001/XMLSchema#string

P2860

RNA-guided human genome engineering via Cas9

Cpf1 is a single RNA-guided endonuclease of a class 2 CRISPR-Cas system

Characterization of dystrophin deficient rats: a new model for Duchenne muscular dystrophy

ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering

Genetic screens in human cells using the CRISPR-Cas9 system

CRISPR-mediated Genome Editing Restores Dystrophin Expression and Function in mdx Mice

Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy

A novel custom high density-comparative genomic hybridization array detects common rearrangements as well as deep intronic mutations in dystrophinopathies.

Assessment of the feasibility of exon 45-55 multiexon skipping for Duchenne muscular dystrophy

What Can We Learn From Clinical Trials of Exon Skipping for DMD?

P304

11-19

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P31

scholarly article

P356

10.1016/J.OMTN.2017.02.004

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P478

http://www.w3.org/2001/XMLSchema#string

P50

Vincent Mouly

Fulvio Mavilio

Matteo Bovolenta

P577

2017-02-10T00:00:00Z

http://www.w3.org/2001/XMLSchema#dateTime

P698

28624187

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P921

myoblast

CRISPR

P932

5363679

http://www.w3.org/2001/XMLSchema#string

Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.

about

P2860

P2860

Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.

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P1433

P1476

P2093

P2860

P304

P31

P356

P478

P50

P577

P698

P921

P932

P356

P1433

P1476

P2093

P2860

P304

P31

P356

P478

P50

P577

P698

P921

P932