Functional Gene Correction for Cystic Fibrosis in Lung Epithelial Cells Generated from Patient iPSCs.
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Human induced pluripotent stem cells for monogenic disease modelling and therapyCustomizing the genome as therapy for the β-hemoglobinopathiesThe Rise of CRISPR/Cas for Genome Editing in Stem CellsGenome-editing Technologies for Gene and Cell TherapyLinking bronchopulmonary dysplasia to adult chronic lung diseases: role of WNT signalingBarriers to inhaled gene therapy of obstructive lung diseases: A reviewInduced Pluripotent Stem Cells Meet Genome EditingApplications of CRISPR technologies in research and beyond.Partial Restoration of CFTR Function in cftr-Null Mice following Targeted Cell Replacement Therapy.Hallmarks of therapeutic management of the cystic fibrosis functional landscape.Tissue Engineering and Regenerative Medicine 2015: A Year in ReviewGenome Editing of the CYP1A1 Locus in iPSCs as a Platform to Map AHR Expression throughout Human Development.TALENs Facilitate Single-step Seamless SDF Correction of F508del CFTR in Airway Epithelial Submucosal Gland Cell-derived CF-iPSCs.CRISPR-Cas9: a promising tool for gene editing on induced pluripotent stem cells.Proceedings: Regenerative Medicine for Lung Diseases: A CIRM Workshop Report.Gene-targeting pharmaceuticals for single-gene disorders.Current Progress in Therapeutic Gene Editing for Monogenic DiseasesIn Vitro Models to Study Human Lung Development, Disease and Homeostasis.Applications of CRISPR genome editing technology in drug target identification and validation.CRISPR/Cas9-Mediated Three Nucleotide Insertion Corrects a Deletion Mutation in MRP1/ABCC1 and Restores Its Proper Folding and Function.What rheumatologists need to know about CRISPR/Cas9.Genetic medicines for CF: Hype versus reality.An Official American Thoracic Society Workshop Report 2015. Stem Cells and Cell Therapies in Lung Biology and Diseases.Genome engineering tools for building cellular models of disease.Gene correction in patient-specific iPSCs for therapy development and disease modeling.Impact of gene editing on the study of cystic fibrosis.Therapeutic applications of CRISPR RNA-guided genome editing.Induced pluripotent stem cell technology: a decade of progress.The discovery and development of the CRISPR system in applications in genome manipulation.May I Cut in? Gene Editing Approaches in Human Induced Pluripotent Stem Cells.Stem cell-derived organoids and their application for medical research and patient treatment.Therapeutic gene editing: delivery and regulatory perspectivesGenome editing: a robust technology for human stem cells.Toward a CRISPR Picture: Use of CRISPR/Cas9 to Model Diseases in Human Stem Cells In Vitro.Gene editing advance re-ignites debate on the merits and risks of animal to human transplantation.Analysis of gene repair tracts from Cas9/gRNA double-stranded breaks in the human CFTR gene.Gene Editing with Helper-Dependent Adenovirus Can Efficiently Introduce Multiple Changes Simultaneously over a Large Genomic Region.Fixing stem cells via genome editing: hope for cystic fibrosis?Addressing challenges in the clinical applications associated with CRISPR/Cas9 technology and ethical questions to prevent its misuse.The Future of CRISPR Applications in the Lab, the Clinic and Society.
P2860
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P2860
Functional Gene Correction for Cystic Fibrosis in Lung Epithelial Cells Generated from Patient iPSCs.
description
2015 nî lūn-bûn
@nan
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
2015年论文
@zh
2015年论文
@zh-cn
name
Functional Gene Correction for ...... Generated from Patient iPSCs.
@en
Functional Gene Correction for ...... Generated from Patient iPSCs.
@nl
type
label
Functional Gene Correction for ...... Generated from Patient iPSCs.
@en
Functional Gene Correction for ...... Generated from Patient iPSCs.
@nl
prefLabel
Functional Gene Correction for ...... Generated from Patient iPSCs.
@en
Functional Gene Correction for ...... Generated from Patient iPSCs.
@nl
P2093
P2860
P1433
P1476
Functional Gene Correction for ...... Generated from Patient iPSCs.
@en
P2093
Ajai Khanna
Amy L Firth
Carl T Dargitz
Fred H Gage
Gregory S Parker
Inder M Verma
Susan J Qualls
Tushar Menon
P2860
P304
P356
10.1016/J.CELREP.2015.07.062
P577
2015-08-19T00:00:00Z