about
Hematopoietic stem cell engineering at a crossroadsRetroviral vectors and transposons for stable gene therapy: advances, current challenges and perspectivesDynamics of HSPC repopulation in nonhuman primates revealed by a decade-long clonal-tracking study.Stable transgene expression in primitive human CD34+ hematopoietic stem/progenitor cells, using the Sleeping Beauty transposon systemEvaluation of biolistic gene transfer methods in vivo using non-invasive bioluminescent imaging techniquesMethodology and software to detect viral integration site hot-spots.Ethics. Gene doping and sport.Correct mRNA processing at a mutant TT splice donor in FANCC ameliorates the clinical phenotype in patients and is enhanced by delivery of suppressor U1 snRNAs.Genomic discovery of potent chromatin insulators for human gene therapy.Integration profile of retroviral vector in gene therapy treated patients is cell-specific according to gene expression and chromatin conformation of target cellPotential renovascular hypertension, space missions, and the role of magnesium.Long space missions, gene therapy, and the vital role of magnesium: a three-pronged plan for the next 50 yearsDifferential Secondary Reconstitution of In Vivo-Selected Human SCID-Repopulating Cells in NOD/SCID versus NOD/SCID/γ chain Mice.Live and let die: a new suicide gene therapy moves to the clinicIntracellular transport of recombinant adeno-associated virus vectors.Metabolic correction of congenital erythropoietic porphyria with iPSCs free of reprogramming factors.Catching the engram: strategies to examine the memory trace.Musings on genome medicine: gene therapy.Retroviral vectors for gene therapy.Ex vivo gene transfer and correction for cell-based therapies.Branched and linear poly(ethylene imine)-based conjugates: synthetic modification, characterization, and application.Recent developments and perspectives on gene therapy using synthetic vectors.Genome editing of the germline: broadening the discussion.Modification of hematopoietic stem/progenitor cells with CD19-specific chimeric antigen receptors as a novel approach for cancer immunotherapy.Targeting MOG expression to dendritic cells delays onset of experimental autoimmune disease.Chemoprotection of human hematopoietic stem cells by simultaneous lentiviral overexpression of multidrug resistance 1 and O(6)-methylguanine-DNA methyltransferase(P140K).Expectations and beliefs in science communication: Learning from three European gene therapy discussions of the early 1990s.Therapeutic levels of erythropoietin (EPO) achieved after gene electrotransfer to skin in mice.High-throughput screening-based selection and scale-up of aqueous two-phase systems for pDNA purification.Consequentialism and the Synthetic Biology Problem.The position of the AUG start codon in MFG-based γ-retroviral vectors has a dramatic effect on translation-dependent protein expression.A multifunctional nanocomplex for enhanced cell uptake, endosomal escape and improved cancer therapeutic effect.
P2860
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P2860
description
2009 nî lūn-bûn
@nan
2009年の論文
@ja
2009年学术文章
@wuu
2009年学术文章
@zh-cn
2009年学术文章
@zh-hans
2009年学术文章
@zh-my
2009年学术文章
@zh-sg
2009年學術文章
@yue
2009年學術文章
@zh
2009年學術文章
@zh-hant
name
Gene therapy fulfilling its promise.
@en
Gene therapy fulfilling its promise.
@nl
type
label
Gene therapy fulfilling its promise.
@en
Gene therapy fulfilling its promise.
@nl
prefLabel
Gene therapy fulfilling its promise.
@en
Gene therapy fulfilling its promise.
@nl
P356
P1476
Gene therapy fulfilling its promise.
@en
P2093
Fabio Candotti
P304
P356
10.1056/NEJME0809614
P407
P577
2009-01-01T00:00:00Z