Application of SFHR to gene therapy of monogenic disorders.
about
Gene therapy for sickle cell diseaseGene therapy for sickle cell diseaseGene therapy for sickle cell diseaseOligo/polynucleotide-based gene modification: strategies and therapeutic potentialA comparison of synthetic oligodeoxynucleotides, DNA fragments and AAV-1 for targeted episomal and chromosomal gene repairSmall fragment homologous replacement: evaluation of factors influencing modification efficiency in an eukaryotic assay system.Nanoparticles deliver triplex-forming PNAs for site-specific genomic recombination in CD34+ human hematopoietic progenitors.Gene therapy for sickle cell disease.Targeted genetic repair: an emerging approach to genetic therapy.Sequence-specific modification of genomic DNA by small DNA fragmentsIllegitimate DNA integration in mammalian cells.Cftr gene targeting in mouse embryonic stem cells mediated by Small Fragment Homologous Replacement (SFHR)Systemic delivery of triplex-forming PNA and donor DNA by nanoparticles mediates site-specific genome editing of human hematopoietic cells in vivo.Targeted correction of single-base-pair mutations with adeno-associated virus vectors under nonselective conditions.An update on targeted gene repair in mammalian cells: methods and mechanismsThe Gene Targeting Approach of Small Fragment Homologous Replacement (SFHR) Alters the Expression Patterns of DNA Repair and Cell Cycle Control Genes.Use of genome-editing tools to treat sickle cell disease.Multiple copies of a linear donor fragment released in situ from a vector improve the efficiency of zinc-finger nuclease-mediated genome editing.Site-specific base changes in the coding or promoter region of the human beta- and gamma-globin genes by single-stranded oligonucleotides.Nuclease-mediated double-strand break (DSB) enhancement of small fragment homologous recombination (SFHR) gene modification in human-induced pluripotent stem cells (hiPSCs)Sequence-specific correction of genomic hypoxanthine-guanine phosphoribosyl transferase mutations in lymphoblasts by small fragment homologous replacement.A LacZ-based transgenic mouse for detection of somatic gene repair events in vivo.Modification of the pig CFTR gene mediated by small fragment homologous replacement.
P2860
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P2860
Application of SFHR to gene therapy of monogenic disorders.
description
2002 nî lūn-bûn
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2002年の論文
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2002年学术文章
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2002年学术文章
@zh-cn
2002年学术文章
@zh-hans
2002年学术文章
@zh-my
2002年学术文章
@zh-sg
2002年學術文章
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2002年學術文章
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2002年學術文章
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name
Application of SFHR to gene therapy of monogenic disorders.
@en
Application of SFHR to gene therapy of monogenic disorders.
@nl
type
label
Application of SFHR to gene therapy of monogenic disorders.
@en
Application of SFHR to gene therapy of monogenic disorders.
@nl
prefLabel
Application of SFHR to gene therapy of monogenic disorders.
@en
Application of SFHR to gene therapy of monogenic disorders.
@nl
P2093
P356
P1433
P1476
Application of SFHR to gene therapy of monogenic disorders.
@en
P2093
P2888
P304
P356
10.1038/SJ.GT.3301743
P577
2002-06-01T00:00:00Z
P5875
P6179
1036159038