about
The Cohesin Release Factor WAPL Restricts Chromatin Loop ExtensionEasy quantitative assessment of genome editing by sequence trace decomposition.Forebrain ependymal cells are Notch-dependent and generate neuroblasts and astrocytes after stroke.Genome-wide maps of nuclear lamina interactions in single human cellsMechanisms and dynamics of nuclear lamina-genome interactions.Single-cell dynamics of genome-nuclear lamina interactions.A double-switch vector system positively regulates transgene expression by endogenous microRNA expression (miR-ON vector).Regulated and multiple miRNA and siRNA delivery into primary cells by a lentiviral platform.Oxidative stress and cell death in cells expressing L-ferritin variants causing neuroferritinopathy.Stable knockdown of microRNA in vivo by lentiviral vectors.Generation of potent and stable human CD4+ T regulatory cells by activation-independent expression of FOXP3.Efficient Tet-dependent expression of human factor IX in vivo by a new self-regulating lentiviral vector.Coordinate dual-gene transgenesis by lentiviral vectors carrying synthetic bidirectional promoters.Nuclear lamins are not required for lamina-associated domain organization in mouse embryonic stem cells.Widespread enzymatic correction of CNS tissues by a single intracerebral injection of therapeutic lentiviral vector in leukodystrophy mouse models.Identification of hematopoietic stem cell-specific miRNAs enables gene therapy of globoid cell leukodystrophy.Endogenous microRNA can be broadly exploited to regulate transgene expression according to tissue, lineage and differentiation state.Reprogramming T lymphocytes for melanoma adoptive immunotherapy by T-cell receptor gene transfer with lentiviral vectors.Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locus.Forkhead box protein 3 (FOXP3) mutations lead to increased TH17 cell numbers and regulatory T-cell instabilityEffects of phosphorylation and neuronal activity on the control of synapse formation by synapsin IEditing a γ-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotypeOptimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements
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P50
description
researcher
@en
wetenschapper
@nl
հետազոտող
@hy
name
Mario Amendola
@ast
Mario Amendola
@en
Mario Amendola
@es
Mario Amendola
@nl
type
label
Mario Amendola
@ast
Mario Amendola
@en
Mario Amendola
@es
Mario Amendola
@nl
prefLabel
Mario Amendola
@ast
Mario Amendola
@en
Mario Amendola
@es
Mario Amendola
@nl
P106
P21
P31
P496
0000-0002-1188-8856