about
In vivo genome editing restores haemostasis in a mouse model of haemophiliaIn vivo genome editing of the albumin locus as a platform for protein replacement therapyPreclinical evaluation of an anti-HCV miRNA cluster for treatment of HCV infectionAdeno-associated viral vectors for the treatment of hemophilia.Robust ZFN-mediated genome editing in adult hemophilic mice.Skeletal muscle metabolism in the pathology and treatment of type 1 diabetes.Overcoming preexisting humoral immunity to AAV using capsid decoysAn edible switch for gene therapy.Reversal of type 1 diabetes by engineering a glucose sensor in skeletal muscle.Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant.Entering the Modern Era of Gene Therapy
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Q28241725-6B9E25CA-EBA4-4CED-9527-AC978C9121F4Q36143241-D686D6DD-90E8-454A-8550-EB89D2A0FE79Q36659298-910D0EB2-CB2E-4BBE-BF4B-C3A140D5D0F0Q36713767-06CF6DD0-3A12-41F1-9B40-74A7B11BC424Q37291607-B79E539B-0056-42A3-B6C4-C762DE4DA89EQ37664811-389FA19C-03B0-4382-954E-39FE17E065D5Q42056009-F75080B6-D468-459E-991F-34BAA3F3A963Q45857240-906511C2-0347-42D2-AF8A-E793177ABBFBQ45858699-5922C5AA-3B40-43B9-A4C9-5440EF3CD3D3Q45875499-647310B7-DCF5-4CDC-882E-8AA6E5AB9D02Q93377068-B10A12B9-3CC6-4E96-B53F-972EE9B1E064
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description
researcher
@en
wetenschapper
@nl
հետազոտող
@hy
name
Xavier M Anguela
@ast
Xavier M Anguela
@en
Xavier M Anguela
@es
Xavier M Anguela
@nl
type
label
Xavier M Anguela
@ast
Xavier M Anguela
@en
Xavier M Anguela
@es
Xavier M Anguela
@nl
prefLabel
Xavier M Anguela
@ast
Xavier M Anguela
@en
Xavier M Anguela
@es
Xavier M Anguela
@nl
P106
P21
P31
P496
0000-0003-2430-8598