about
CNS-directed gene therapy for the treatment of neurologic and somatic mucopolysaccharidosis type II (Hunter syndrome)Whole body correction of mucopolysaccharidosis IIIA by intracerebrospinal fluid gene therapyInsulin-like growth factor I (IGF-I)-induced chronic gliosis and retinal stress lead to neurodegeneration in a mouse model of retinopathyProgressive neurologic and somatic disease in a novel mouse model of human mucopolysaccharidosis type IIIC.In vivo adeno-associated viral vector-mediated genetic engineering of white and brown adipose tissue in adult mice.Disease correction by AAV-mediated gene therapy in a new mouse model of mucopolysaccharidosis type IIID.AAV8-mediated Sirt1 gene transfer to the liver prevents high carbohydrate diet-induced nonalcoholic fatty liver disease.Biochemical, histological and functional correction of mucopolysaccharidosis type IIIB by intra-cerebrospinal fluid gene therapy.FGF21 gene therapy as treatment for obesity and insulin resistance
P50
Q27333793-7E47D757-731D-4ACE-9BF6-6002888FC03AQ30541880-C712E688-F6DB-475F-83FC-4B7A9C088E4DQ36929063-54B71F9F-DB55-431C-892B-17C29747F461Q37305882-96DBC4AB-BB88-47B8-B5E3-3154B144205EQ39348746-3D8C82FA-49BF-443E-B98E-36328E85D403Q40277701-FD0A0C69-05EE-426C-BC8A-D733488AFA3FQ42085309-9212467B-01C9-4640-B406-C162C371EF6EQ42176546-ED29F136-5ED4-47EB-AA0D-3A528FFC039EQ57688659-3968D1C3-1D09-448C-952B-6056A8A0ABBE
P50
description
investigador
@es
researcher
@en
wetenschapper
@nl
name
Albert Ribera
@en
Albert Ribera
@nl
type
label
Albert Ribera
@en
Albert Ribera
@nl
prefLabel
Albert Ribera
@en
Albert Ribera
@nl
P31
P496
0000-0002-7120-4276