about
CNS-directed gene therapy for the treatment of neurologic and somatic mucopolysaccharidosis type II (Hunter syndrome)Progressive neurologic and somatic disease in a novel mouse model of human mucopolysaccharidosis type IIIC.Disease correction by AAV-mediated gene therapy in a new mouse model of mucopolysaccharidosis type IIID.
P50
description
investigador
@es
researcher
@en
name
Joan Bertolin
@en
type
label
Joan Bertolin
@en
prefLabel
Joan Bertolin
@en
P31
P496
0000-0002-5196-0955