The Expanded Access Use of Viltolarsen in Duchenne Muscular Dystrophy With Confirmed Exon 53 Amenable Mutation
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The Expanded Access Use of Viltolarsen in Duchenne Muscular Dystrophy With Confirmed Exon 53 Amenable Mutation
description
clinical trial
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ensayo clínico
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klinisch onderzoek
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name
The Expanded Access Use of Vil ...... rmed Exon 53 Amenable Mutation
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type
label
The Expanded Access Use of Vil ...... rmed Exon 53 Amenable Mutation
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prefLabel
The Expanded Access Use of Vil ...... rmed Exon 53 Amenable Mutation
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P921
P1476
The Expanded Access Use of Vil ...... ) Amenable to Exon 53 Skipping
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P3098
NCT04337112